共 17 条
- [1] Antisense and siRNA as agonists of Toll-like receptors[J]. NATURE BIOTECHNOLOGY, 2004, 22 (12) : 1533 - 1537Agrawal, S论文数: 0 引用数: 0 h-index: 0机构: Hybridon Inc, Cambridge, MA 02139 USA Hybridon Inc, Cambridge, MA 02139 USAKandimalla, ER论文数: 0 引用数: 0 h-index: 0机构: Hybridon Inc, Cambridge, MA 02139 USA Hybridon Inc, Cambridge, MA 02139 USA
- [2] OLIGODEOXYNUCLEOSIDE PHOSPHORAMIDATES AND PHOSPHOROTHIOATES AS INHIBITORS OF HUMAN IMMUNODEFICIENCY VIRUS[J]. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1988, 85 (19) : 7079 - 7083AGRAWAL, S论文数: 0 引用数: 0 h-index: 0机构: NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892 NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892GOODCHILD, J论文数: 0 引用数: 0 h-index: 0机构: NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892 NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892CIVEIRA, MP论文数: 0 引用数: 0 h-index: 0机构: NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892 NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892THORNTON, AH论文数: 0 引用数: 0 h-index: 0机构: NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892 NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892SARIN, PS论文数: 0 引用数: 0 h-index: 0机构: NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892 NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892ZAMECNIK, PC论文数: 0 引用数: 0 h-index: 0机构: NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892 NCI,TUMOR CELL BIOL LAB,BETHESDA,MD 20892
- [3] Agrawal S., 2019, Advances in Nucleic Acid Therapeutics
- [4] CRICK F H, 1958, Symp Soc Exp Biol, V12, P138
- [5] Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy[J]. NEW ENGLAND JOURNAL OF MEDICINE, 2017, 377 (18) : 1723 - 1732Finkel, R. S.论文数: 0 引用数: 0 h-index: 0机构: Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAMercuri, E.论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USADarras, B. T.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Dept Neurol, Boston, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAConnolly, A. M.论文数: 0 引用数: 0 h-index: 0机构: St Louis Childrens Hosp, Dept Neurol, St Louis, MO 63178 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAKuntz, N. L.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp Chicago, Dept Pediat, Chicago, IL 60611 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAKirschner, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Fac Med, Med Ctr, Dept Neuropediat & Muscle Disorders, Freiburg, Germany Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAChiriboga, C. A.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Neurol, New York, NY USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USASaito, K.论文数: 0 引用数: 0 h-index: 0机构: Tokyo Womens Med Coll, Inst Med Genet, Tokyo, Japan Tokyo Womens Med Coll, Dept Pediat, Tokyo, Japan Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAServais, L.论文数: 0 引用数: 0 h-index: 0机构: Inst Mot, Paris, France Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USATizzano, E.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Vall dHebron, Dept Clin & Mol Genet, Barcelona, Spain Univ Hosp Vall dHebron, Rare Dis Unit, Barcelona, Spain Ctr Invest Biomed Enfermedades Raras CIBERER, Barcelona, Spain Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USATopaloglu, H.论文数: 0 引用数: 0 h-index: 0机构: Hacettepe Univ, Sch Med, Dept Pediat, Ankara, Turkey Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USATulinius, M.论文数: 0 引用数: 0 h-index: 0机构: Gothenburg Univ, Queen Silvia Childrens Hosp, Dept Pediat, Gothenburg, Sweden Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAMontes, J.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Neurol, New York, NY USA Columbia Univ, Dept Rehabil & Regenerat Med, New York, NY USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAGlanzman, A. M.论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Dept Phys Therapy, Philadelphia, PA 19104 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USABishop, K.论文数: 0 引用数: 0 h-index: 0机构: lonis Pharmaceut, Carlsbad, CA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAZhong, Z. J.论文数: 0 引用数: 0 h-index: 0机构: Biogen, Cambridge, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAGheuens, S.论文数: 0 引用数: 0 h-index: 0机构: Biogen, Cambridge, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USABennett, C. F.论文数: 0 引用数: 0 h-index: 0机构: lonis Pharmaceut, Carlsbad, CA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USASchneider, E.论文数: 0 引用数: 0 h-index: 0机构: lonis Pharmaceut, Carlsbad, CA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USAFarwell, W.论文数: 0 引用数: 0 h-index: 0机构: Biogen, Cambridge, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USADe Vivo, D. C.论文数: 0 引用数: 0 h-index: 0机构: Columbia Univ, Dept Neurol, Med Ctr, New York, NY USA Columbia Univ, Dept Pediat, Med Ctr, New York, NY 10027 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA
- [6] COMPLEMENT ACTIVATION AND HEMODYNAMIC-CHANGES FOLLOWING INTRAVENOUS ADMINISTRATION OF PHOSPHOROTHIOATE OLIGONUCLEOTIDES IN THE MONKEY[J]. ANTISENSE RESEARCH AND DEVELOPMENT, 1994, 4 (03): : 201 - 206GALBRAITH, WM论文数: 0 引用数: 0 h-index: 0机构: APD CO,ARLINGTON,VA 22209HOBSON, WC论文数: 0 引用数: 0 h-index: 0机构: APD CO,ARLINGTON,VA 22209GICLAS, PC论文数: 0 引用数: 0 h-index: 0机构: APD CO,ARLINGTON,VA 22209SCHECHTER, PJ论文数: 0 引用数: 0 h-index: 0机构: APD CO,ARLINGTON,VA 22209AGRAWAL, S论文数: 0 引用数: 0 h-index: 0机构: APD CO,ARLINGTON,VA 22209
- [7] Patient-Customized Oligonucleotide Therapy for a Rare Genetic Disease[J]. NEW ENGLAND JOURNAL OF MEDICINE, 2019, 381 (17) : 1644 - 1652Kim, J.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Dept Biomed Informat, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USAHu, C.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Div Genet & Genom, Boston, MA USAEl Achkar, C. Moufawad论文数: 0 引用数: 0 h-index: 0机构: Dept Neurol, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USABlack, L. E.论文数: 0 引用数: 0 h-index: 0机构: Charles River Labs, Wilmington, MA USA Div Genet & Genom, Boston, MA USADouville, J.论文数: 0 引用数: 0 h-index: 0机构: Charles River Labs, Montreal, PQ, Canada Div Genet & Genom, Boston, MA USALarson, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Colorado, Sch Med, Aurora, CO USA Div Genet & Genom, Boston, MA USAPendergast, M. K.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USAGoldkind, S. F.论文数: 0 引用数: 0 h-index: 0机构: Goldkind Consulting, Potomac, MD USA Div Genet & Genom, Boston, MA USALee, E. A.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Broad Inst MIT & Harvard, Cambridge, MA 02142 USA Div Genet & Genom, Boston, MA USAKuniholm, A.论文数: 0 引用数: 0 h-index: 0机构: Inst Ctr Clin & Translat Res, Boston, MA USA Boston Childrens Hosp, Boston, MA USA Boston Childrens, Boston, MA USA Dana Farber Canc, Boston, MA USA Blood Disorders Ctr, Boston, MA USA Div Genet & Genom, Boston, MA USASoucy, A.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Div Genet & Genom, Boston, MA USAVaze, J.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Div Genet & Genom, Boston, MA USABelur, N. R.论文数: 0 引用数: 0 h-index: 0机构: Northwestern Univ, Dept Neurol, Feinberg Sch Med, Chicago, IL 60611 USA Div Genet & Genom, Boston, MA USA论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Tsytsykova, A.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Boston, MA USA Div Genet & Genom, Boston, MA USAArmant, M.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Boston, MA USA Div Genet & Genom, Boston, MA USADiDonato, R. L.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Div Genet & Genom, Boston, MA USAChoi, J.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Div Genet & Genom, Boston, MA USACornelissen, L.论文数: 0 引用数: 0 h-index: 0机构: Dept Anesthesiol, Dept Crit Care & Pain Med, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USAPereira, L. M.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Boston, MA USA Div Genet & Genom, Boston, MA USAAugustine, E. F.论文数: 0 引用数: 0 h-index: 0机构: Univ Rochester, Med Ctr, Dept Neurol, Rochester, NY 14642 USA Div Genet & Genom, Boston, MA USAGenetti, C. A.论文数: 0 引用数: 0 h-index: 0机构: Manton Ctr Orphan Dis Res, Boston, MA USA Div Genet & Genom, Boston, MA USADies, K.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Boston, MA USA Div Genet & Genom, Boston, MA USABarton, B.论文数: 0 引用数: 0 h-index: 0机构: Inst Ctr Clin & Translat Res, Boston, MA USA Boston Childrens Hosp, Boston, MA USA Boston Childrens, Boston, MA USA Dana Farber Canc, Boston, MA USA Blood Disorders Ctr, Boston, MA USA Div Genet & Genom, Boston, MA USAWilliams, L.论文数: 0 引用数: 0 h-index: 0机构: Inst Ctr Clin & Translat Res, Boston, MA USA Boston Childrens Hosp, Boston, MA USA Boston Childrens, Boston, MA USA Dana Farber Canc, Boston, MA USA Blood Disorders Ctr, Boston, MA USA Div Genet & Genom, Boston, MA USAGoodlett, B. D.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USARiley, B. L.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USAPasternak, A.论文数: 0 引用数: 0 h-index: 0机构: Dept Phys & Occupat Therapy, Boston, MA USA Div Genet & Genom, Boston, MA USABerry, E. R.论文数: 0 引用数: 0 h-index: 0机构: Dept Phys & Occupat Therapy, Boston, MA USA Div Genet & Genom, Boston, MA USAPflock, K. A.论文数: 0 引用数: 0 h-index: 0机构: Dept Phys & Occupat Therapy, Boston, MA USA Pendergast Consulting, Washington, DC USA Div Genet & Genom, Boston, MA USAChu, S.论文数: 0 引用数: 0 h-index: 0机构: Dept Pharm, Boston, MA USA Div Genet & Genom, Boston, MA USAReed, C.论文数: 0 引用数: 0 h-index: 0机构: Brain Hz Consulting, Del Mar, DE USA Div Genet & Genom, Boston, MA USATyndall, K.论文数: 0 引用数: 0 h-index: 0机构: Tyndall Consulting, Wake Forest, NC USA Div Genet & Genom, Boston, MA USAAgrawal, P. B.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Div Newborn Med, Boston, MA USA Manton Ctr Orphan Dis Res, Boston, MA USA Div Genet & Genom, Boston, MA USABeggs, A. H.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Manton Ctr Orphan Dis Res, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USAGrant, P. E.论文数: 0 引用数: 0 h-index: 0机构: Div Newborn Med, Boston, MA USA Div Neuroradiol, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USAUrion, D. K.论文数: 0 引用数: 0 h-index: 0机构: Dept Neurol, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USASnyder, R. O.论文数: 0 引用数: 0 h-index: 0机构: Brammer Bio, Alachua, FL USA Div Genet & Genom, Boston, MA USAWaisbren, S. E.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USAPoduri, A.论文数: 0 引用数: 0 h-index: 0机构: Dept Neurol, Boston, MA USA Div Genet & Genom, Boston, MA USAPark, P. J.论文数: 0 引用数: 0 h-index: 0机构: Dept Biomed Informat, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USAPatterson, A.论文数: 0 引用数: 0 h-index: 0机构: Dept Pharm, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USABiffi, A.论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Gene Therapy Program, Boston, MA USA Div Genet & Genom, Boston, MA USAMazzulli, J. R.论文数: 0 引用数: 0 h-index: 0机构: Northwestern Univ, Dept Neurol, Feinberg Sch Med, Chicago, IL 60611 USA Div Genet & Genom, Boston, MA USABodamer, O.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Broad Inst MIT & Harvard, Cambridge, MA 02142 USA Div Genet & Genom, Boston, MA USABerde, C. B.论文数: 0 引用数: 0 h-index: 0机构: Dept Anesthesiol, Dept Crit Care & Pain Med, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Div Genet & Genom, Boston, MA USAYu, T. W.论文数: 0 引用数: 0 h-index: 0机构: Div Genet & Genom, Boston, MA USA Harvard Med Sch, Boston, MA 02115 USA Broad Inst MIT & Harvard, Cambridge, MA 02142 USA Div Genet & Genom, Boston, MA USA
- [8] Antisense oligonucleotide modulation of non-productive alternative splicing upregulates gene expression[J]. NATURE COMMUNICATIONS, 2020, 11 (01)Lim, Kian Huat论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USAHan, Zhou论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USAJeon, Hyun Yong论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USAKach, Jacob论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USAJing, Enxuan论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USAWeyn-Vanhentenryck, Sebastien论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USADowns, Mikaela论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USACorrionero, Anna论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USAOh, Raymond论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USAScharner, Juergen论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USAVenkatesh, Aditya论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USAJi, Sophina论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USALiau, Gene论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USATicho, Barry论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USANash, Huw论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USAAznarez, Isabel论文数: 0 引用数: 0 h-index: 0机构: Stoke Therapeut Inc, Bedford, MA 01730 USA Stoke Therapeut Inc, Bedford, MA 01730 USA
- [9] Metelev V., Patent No. [US6346614, 6346614]
- [10] Metelev V., Patent No. [US5652355, 5652355]