FOXP3 Gene Transfer in T cells and FOXP3 Gene Editing in HSC as Novel Treatment Options for IPEX Syndrome

被引：0
|
作者：
Goodwin, Marianne [1 ]
Sato, Yohei [1 ]
Passerini, Laura [2 ]
Barzaghi, Federica [2 ]
Lee, Esmond [3 ]
Suzette, Shipp K. [1 ]
Roncarolo, Maria Grazia [4 ,5 ,6 ]
Porteus, Matthew [1 ]
Bacchetta, Rosa [1 ]
机构：
[1] Stanford Univ, Sch Med, Dept Pediat, Div Stem Cell Transplantat & Regenerat Med, Stanford, CA 94305 USA
[2] Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Div Regenerat Med Stem Cells & Gene Therapy, Milan, Italy
[3] Stanford Univ, Sch Med, Inst Stem Cell Biol & Regenerat Med, Stanford, CA 94305 USA
[4] Stanford Univ, Sch Med, Pediat Stem Cell Transplantat & Regenerat Med & M, Stanford, CA 94305 USA
[5] Stanford Univ, Sch Med, Pediat Stem Cell Transplantat & Regenerat Med, Stanford, CA 94305 USA
[6] Stanford Univ, Sch Med, Div Stem Cell Transplantat & Regenerat Med, Ctr Definit & Curat Med,Dept Pediat, Stanford, CA 94305 USA
来源：
JOURNAL OF CLINICAL IMMUNOLOGY | 2018年 / 38卷 / 03期
关键词：
D O I：
暂无
中图分类号：
R392 [医学免疫学]; Q939.91 [免疫学];
学科分类号：
100102 ;
摘要：
引用
收藏
页码：427 / 427
页数：1
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