Allele-Specific Repression of Mutant Huntingtin Expression By Engineered Zinc Finger Transcriptional Repressors as a Potential Therapy for Huntington's Disease

被引：0
|
作者：
Zeitler, Bryan [1 ]
Froelich, Steven [1 ]
Yu, Qi [1 ]
Pearl, Jocelynn [1 ]
Paschon, David E. [1 ]
Miller, Jeffrey C. [1 ]
Li, Davis [1 ]
Marlen, Kimberly [1 ]
Guschin, Dmitry [1 ]
Zhang, Lei [1 ]
Mendel, Matthew [1 ]
Munoz-Sanjuan, Ignacio [2 ]
Rebar, Edward J. [1 ]
Urnov, Fyodor D. [1 ]
Gregory, Philip D. [1 ]
Zhang, H. Steve [1 ]
机构：
[1] Sangamo BioSci Inc, Richmond, CA USA
[2] CHDI Fdn Inc, Los Angeles, CA USA
来源：
MOLECULAR THERAPY | 2014年 / 22卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
603
引用
收藏
页码：S233 / S233
页数：1
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