Allele-Specific Repression of Mutant Huntingtin Expression By Engineered Zinc Finger Transcriptional Repressors as a Potential Therapy for Huntington's Disease

被引：0

作者：

Zeitler, Bryan ^{[1
]}

Froelich, Steven ^{[1
]}

Yu, Qi ^{[1
]}

Pearl, Jocelynn ^{[1
]}

Paschon, David E. ^{[1
]}

Miller, Jeffrey C. ^{[1
]}

Li, Davis ^{[1
]}

Marlen, Kimberly ^{[1
]}

Guschin, Dmitry ^{[1
]}

Zhang, Lei ^{[1
]}

Mendel, Matthew ^{[1
]}

Munoz-Sanjuan, Ignacio ^{[2
]}

Rebar, Edward J. ^{[1
]}

Urnov, Fyodor D. ^{[1
]}

Gregory, Philip D. ^{[1
]}

Zhang, H. Steve ^{[1
]}

机构：

[1] Sangamo BioSci Inc, Richmond, CA USA

[2] CHDI Fdn Inc, Los Angeles, CA USA

来源：

MOLECULAR THERAPY | 2014年 / 22卷

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

603

引用

页码：S233 / S233

页数：1

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