Outcomes of Patients with Hereditary Transthyretin-Mediated Amyloidosis with Early Onset V30M versus all other Mutations in APOLLO, a Phase 3 Study of Patisiran

被引：0

作者：

Coelho, T.

Adams, D. ^{[1
]}

Gonzalez-Duarte, A. ^{[2
]}

O'riordan, W. ^{[3
]}

Yang, C. -C. ^{[4
]}

Yamashita, T. ^{[5
]}

Kristen, A. ^{[6
]}

Tournev, I. ^{[7
]}

Schmidt, H. ^{[8
]}

Berk, J. ^{[9
]}

Lin, K. -P. ^{[10
]}

Gandhi, P. ^{[11
]}

Sweetser, M. ^{[11
]}

White, M. ^{[11
]}

Goyal, S. ^{[11
]}

Gollob, J. ^{[11
]}

Suhr, O.

机构：

[1] CHU Bicetre, Neurol Adulte NNERF, French Reference Ctr FAP & Other Rare Peripheral, Le Kremlin Bicetre, France

[2] Natl Inst Med Sci & Nutr Salvador Zubiran INCMNSZ, Mexico City, DF, Mexico

[3] EStudy Site, Lamesa, CA USA

[4] Natl Taiwan Univ Hosp, Taipei, Taiwan

[5] Kumamoto Univ Hosp, Kumamoto, Japan

[6] Heidelberg Univ Hosp, Heidelberg, Germany

[7] New Bulgarian Univ, Dept Cognit Sci & Psychol, Sofia Med Univ, Dept Neurol,Univ Hosp Alexandrovska, Sofia, Bulgaria

[8] Univ Klinikum Munster, Munster, Germany

[9] Boston Univ, Boston, MA 02215 USA

[10] Taipei Vet Gen Hosp, Taipei, Taiwan

[11] Alnylam Pharmaceut, Cambridge, MA USA

来源：

EUROPEAN JOURNAL OF NEUROLOGY | 2018年 / 25卷

关键词：

D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

EPR1138

引用

页码：353 / 354

页数：2

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