Improving CRISPR Genome Editing by Engineering Guide RNAs

被引:72
作者
Moon, Su Bin [1 ,2 ]
Kim, Do Yon [1 ,2 ]
Ko, Jeong-Heon [1 ,2 ]
Kim, Jin-Soo [3 ,4 ,5 ]
Kim, Yong-Sam [1 ,2 ]
机构
[1] KRIBB, Genome Editing Res Ctr, Daejeon, South Korea
[2] Korea Univ Sci & Technol UST, KRIBB Sch Biosci, Daejeon, South Korea
[3] Ctr Genome Engn, Inst Basic Sci, Daejeon, South Korea
[4] Korea Univ Sci & Technol UST, IBS Sch, Daejeon, South Korea
[5] Seoul Natl Univ, Dept Chem, Seoul, South Korea
关键词
CHEMICAL-MODIFICATIONS; MAMMALIAN-CELLS; GENE KNOCKOUT; CAS9; DNA; SPECIFICITY; CPF1; ACTIVATION; BASE; ENDONUCLEASES;
D O I
10.1016/j.tibtech.2019.01.009
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
CRISPR technology is a two-component gene editing system in which the effector protein induces genetic alterations with the aid of a gene targeting guide RNA. Guide RNA can be produced through chemical synthesis, in vitro transcription, or intracellular transcription. Guide RNAs can be engineered to have chemical modifications, alterations in the spacer length, sequence modifications, fusion of RNA or DNA components, and incorporation of deoxynucleotides. Engineered guide RNA can improve genome editing efficiency and target specificity, regulation of biological toxicity, sensitive and specific molecular imaging, multiplexing, and editing flexibility. Therefore, engineered guide RNA will enable more specific, efficient, and safe gene editing, ultimately improving the clinical benefits of gene therapy.
引用
收藏
页码:870 / 881
页数:12
相关论文
共 93 条
  • [1] RNA targeting with CRISPR-Cas13
    Abudayyeh, Omar O.
    Gootenberg, Jonathan S.
    Essletzbichler, Patrick
    Han, Shuo
    Joung, Julia
    Belanto, Joseph J.
    Verdine, Vanessa
    Cox, David B. T.
    Kellner, Max J.
    Regev, Aviv
    Lander, Eric S.
    Voytas, Daniel F.
    Ting, Alice Y.
    Zhang, Feng
    [J]. NATURE, 2017, 550 (7675) : 280 - +
  • [2] The CRISPR tool kit for genome editing and beyond
    Adli, Mazhar
    [J]. NATURE COMMUNICATIONS, 2018, 9
  • [3] Comparative overview of RNA polymerase II and III transcription cycles, with focus on RNA polymerase III termination and reinitiation
    Arimbasseri, Aneeshkumar G.
    Rijal, Keshab
    Maraia, Richard J.
    [J]. TRANSCRIPTION-AUSTIN, 2014, 5 (01): : 1 - 13
  • [4] Minimal 2′-O-methyl phosphorothioate linkage modification pattern of synthetic guide RNAs for increased stability and efficient CRISPR-Cas9 gene editing avoiding cellular toxicity
    Basila, Megan
    Kelley, Melissa L.
    Smith, Anja van Brabant
    [J]. PLOS ONE, 2017, 12 (11):
  • [5] RNA interference in mammalian cells by chemically-modified RNA
    Braasch, DA
    Jensen, S
    Liu, YH
    Kaur, K
    Arar, K
    White, MA
    Corey, DR
    [J]. BIOCHEMISTRY, 2003, 42 (26) : 7967 - 7975
  • [6] Guide RNA Functional Modules Direct Cas9 Activity and Orthogonality
    Briner, Alexandra E.
    Donohoue, Paul D.
    Gomaa, Ahmed A.
    Selle, Kurt
    Slorach, Euan M.
    Nye, Christopher H.
    Haurwitz, Rachel E.
    Beisel, Chase L.
    May, Andrew P.
    Barrangou, Rodolphe
    [J]. MOLECULAR CELL, 2014, 56 (02) : 333 - 339
  • [7] A highly specific SpCas9 variant is identified by in vivo screening in yeast
    Casini, Antonio
    Olivieri, Michele
    Petris, Gianluca
    Montagna, Claudia
    Reginato, Giordano
    Maule, Giulia
    Lorenzin, Francesca
    Prandi, Davide
    Romanel, Alessandro
    Demichelis, Francesca
    Inga, Alberto
    Cereseto, Anna
    [J]. NATURE BIOTECHNOLOGY, 2018, 36 (03) : 265 - +
  • [8] Structural basis for the coevolution of a viral RNA-protein complex
    Chao, Jeffrey A.
    Patskovsky, Yury
    Almo, Steven C.
    Singer, Robert H.
    [J]. NATURE STRUCTURAL & MOLECULAR BIOLOGY, 2008, 15 (01) : 103 - 105
  • [9] Expanding the CRISPR imaging toolset with Staphylococcus aureus Cas9 for simultaneous imaging of multiple genomic loci
    Chen, Baohui
    Hu, Jeffrey
    Almeida, Ricardo
    Liu, Harrison
    Balakrishnan, Sanjeev
    Covill-Cooke, Christian
    Lim, Wendell A.
    Huang, Bo
    [J]. NUCLEIC ACIDS RESEARCH, 2016, 44 (08) : e75
  • [10] Imaging Genomic Elements in Living Cells Using CRISPR/Cas9
    Chen, Baohui
    Huang, Bo
    [J]. USE OF CRISPR/CAS9, ZFNS, AND TALENS IN GENERATING SITE-SPECIFIC GENOME ALTERATIONS, 2014, 546 : 337 - 354