Infusion of Coagulation Factor VIII-Containing Induced Pluripotent Stem Cell (iPSC)-Derived Megakaryocytes (iMks) Shows Potential As Hemophilia a Treatment

被引：2
|
作者：
Lyde, Randolph B., Jr. [1 ,2 ]
Ahn, Hyunsook [3 ]
Vo, Karen K. [1 ,2 ]
Jarocha, Danuta Jadwiga [2 ]
Zhai, Li [4 ]
Sullivan, Spencer K. [5 ]
Arruda, Valder R. [4 ]
Sabatino, Denise E. [6 ]
Camire, Rodney M. [4 ,7 ]
French, Deborah [2 ]
Poncz, Mortimer [2 ,8 ]
机构：
[1] Univ Penn, Sch Med, Pharmacol, Philadelphia, PA USA
[2] Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA USA
[3] Childrens Hosp Philadelphia, Philadelphia, PA USA
[4] Childrens Hosp Philadelphia, Hematol, Philadelphia, PA USA
[5] Mississippi Ctr Adv Med, Madison, MS USA
[6] Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA USA
[7] Univ Penn, Philadelphia, PA USA
[8] Univ Penn, Dept Pediat, Philadelphia, PA USA
来源：
BLOOD | 2016年 / 128卷 / 22期
关键词：
D O I：
10.1182/blood.V128.22.2559.2559
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
2559
引用
收藏
页数：5
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