[1] Med Univ Graz, Graz, Austria
[2] Chaim Sheba Med Ctr, IL-52621 Tel Hashomer, Israel
[3] Shire Human Genet Therapies, Cambridge, MA USA
[4] Barts & London NHS Trust, London, England
[5] Charite, D-13353 Berlin, Germany
[6] Tel Aviv Univ, Tel Aviv Sourasky Med Ctr, IL-69978 Tel Aviv, Israel
[7] Hosp Britan Buenos Aires, Buenos Aires, DF, Argentina