Statistical monitoring of clinical trials with multivariate response and/or multiple arms: a flexible approach

被引:4
|
作者
Zhao, Lihui [1 ]
Hu, X. Joan [1 ]
Lagakos, Stephen W. [2 ]
机构
[1] Simon Fraser Univ, Dept Stat & Actuarial Sci, Burnaby, BC V5A 1S6, Canada
[2] Harvard Univ, Dept Biostat, Sch Publ Hlth, Boston, MA 02115 USA
关键词
Group sequential analysis; Interim review; Multiple comparisons; Multiple end points; Nonparametric inference; Repeated confidence bands; INTERIM ANALYSES; MEAN FUNCTION; END-POINTS;
D O I
10.1093/biostatistics/kxn037
中图分类号
Q [生物科学];
学科分类号
07 ; 0710 ; 09 ;
摘要
Randomized clinical trials with a multivariate response and/or multiple treatment arms are increasingly common, in part because of their efficiency and a greater concern about balancing risks with benefits. In some trials, the specific types and magnitudes of treatment group differences that would warrant early termination cannot easily be specified prior to the onset of the trial and/or could change as the trial progresses. This underscores the need for more flexible monitoring methods than traditional approaches. This paper extends the repeated confidence bands approach for interim monitoring to more general settings where there can be a multivariate response and/or multiple treatment arms and where the metrics for comparing treatment groups can change during the conduct of the trial. We illustrate the approach using the results of a recent AIDS clinical trial and examine its efficiency and robustness via simulation.
引用
收藏
页码:310 / 323
页数:14
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