Efficient Correction of HAX1 Mutations in Primary HSPCs of Severe Congenital Neutropenia Patients Using CRISPR/CAS9 GENE-Editing

被引：2
|
作者：
Ritter, Malte U.
Secker, Benjamin
Nasri, Masoud
Klimiankou, Maksim
Dannenmann, Benjamin
Amend, Diana
Haaf, Jeremy
Mir, Perihan
Bernhard, Regine
Steiert, Ingeborg
Zeidler, Cornelia
Welte, Karl
Skokowa, Julia
机构：
来源：
BLOOD | 2020年 / 136卷
关键词：
D O I：
10.1182/blood-2020-140260
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页数：3
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