Evidence for efficacy and safety of lentiviral mediated gene transfer in T cells and CD34+cells from Wiskott-Aldrich syndrome patients.

被引：0

作者：

Scaramuzza, Samantha

Trifari, Sara

Marangoni, Francesco

Martino, Silvana

Metin, Ayse

Galy, Anne

Naldini, Luigi

Aiuti, Alessandro

Villa, Anna

Dupre, Loic

Roncarolo, Maria Grazia

机构：

[1] San Raffaele Telethon Inst, HSR TIGET, Milan, Italy

[2] Univ Vita Salute San Raffaele, Milan, Italy

[3] Univ Turin, Dept Pediat, I-10124 Turin, Italy

[4] Ankara Univ, Dept Pediat Immunol & Allergy, TR-06100 Ankara, Turkey

[5] Genethon, Evry, France

[6] ITB CNR, Milan, Italy

[7] INSERM, U563, Toulouse, France

来源：

关键词：

D O I：

10.1182/blood.V108.11.3279.3279

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

3279

引用

页码：936A / 936A

页数：1