Correction of Fanconi Anemia Mutation Using the Crispr/Cas9 System

被引:0
|
作者
Kawashima, Nozomu [1 ]
Okuno, Yusuke [1 ]
Sekiya, Yuko [1 ]
Wang, Xinan [1 ]
Narita, Atsushi [1 ]
Doisaki, Sayoko [1 ]
Kamei, Michi [1 ]
Nishio, Nobuhiro [1 ]
Muramatsu, Hideki [1 ]
Hama, Asahito [1 ]
Takahashi, Yoshiyuki [1 ]
Kojima, Seiji [1 ]
机构
[1] Nagoya Univ, Grad Sch Med, Dept Pediat, Nagoya, Aichi 4648601, Japan
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页数:2
相关论文
共 50 条
  • [11] CRISPR/Cas9
    Mizuno, Naoaki
    Mizutani, Eiji
    Sato, Hideyuki
    Kasai, Mariko
    Nakauchi, Hiromitsu
    Yamaguchi, Tomoyuki
    BIO-PROTOCOL, 2019, 9 (13):
  • [12] Targeted mutagenesis in chicken using CRISPR/Cas9 system
    Oishi, Isao
    Yoshii, Kyoko
    Miyahara, Daichi
    Kagami, Hiroshi
    Tagami, Takahiro
    SCIENTIFIC REPORTS, 2016, 6
  • [13] Engineering Citrobacter freundii using CRISPR/Cas9 system
    Alfaro, Trinidad
    Elmore, Joshua R.
    Stromberg, Zachary R.
    Hutchison, Janine R.
    Hess, Becky M.
    JOURNAL OF MICROBIOLOGICAL METHODS, 2022, 200
  • [14] Targeted mutagenesis in chicken using CRISPR/Cas9 system
    Isao Oishi
    Kyoko Yoshii
    Daichi Miyahara
    Hiroshi Kagami
    Takahiro Tagami
    Scientific Reports, 6
  • [15] Targeting Specificity of the CRISPR/Cas9 System
    Tasan, Ipek
    Zhao, Huimin
    ACS SYNTHETIC BIOLOGY, 2017, 6 (09): : 1609 - 1613
  • [16] CRISPR/Cas9 correction of Finnish gyrate atrophy mutation in patient-derived iPSCs
    Maldonado, R.
    Jalil, S.
    Keskinen, T.
    Nieminen, A.
    Hyvonen, M.
    Lapatto, R.
    Wartiovaara, K.
    HUMAN GENE THERAPY, 2021, 32 (19-20) : A69 - A69
  • [17] CRISPR/Cas9 genome editing of RDEB mutation hotspot
    Naso, G.
    Petrova, A.
    Qasim, W.
    HUMAN GENE THERAPY, 2019, 30 (02) : A8 - A8
  • [18] Genetic engineering using CRISPR/Cas9 as a strategy for the treatment of Sickle Cell Anemia
    Danda Vasconcelos Santos, M.
    Nascimento Ferreira, I.
    Silva Dos Santos, F.
    Silva Souza, K.
    Freire Da Silva, M. R.
    Almeida Candido, M.
    Motteran, F.
    Alexandre De Araujo, L. C.
    Melo De Oliveira, M. B.
    CLINICA CHIMICA ACTA, 2024, 558
  • [19] Biallelic editing of a lamprey genome using the CRISPR/Cas9 system
    Yao Zu
    Xushuai Zhang
    Jianfeng Ren
    Xuehong Dong
    Zhe Zhu
    Liang Jia
    Qinghua Zhang
    Weiming Li
    Scientific Reports, 6
  • [20] Using the CRISPR/Cas9 system to understand neuropeptide biology and regulation
    Hay, Elizabeth A.
    Knowles, Christopher
    Kolb, Andreas
    MacKenzie, Alasdair
    NEUROPEPTIDES, 2017, 64 : 19 - 25