Allogeneic hematopoietic stem cell transplant outcomes for patients with dominant negative IKZF1/IKAROS mutations

被引:23
作者
Kellner, Erinn S. [1 ,2 ]
Krupski, Christa [1 ,2 ]
Kuehn, Hye Sun [3 ]
Rosenzweig, Sergio D. [3 ]
Yoshida, Nao [4 ]
Kojima, Seiji [5 ]
Boutboul, David [6 ,7 ]
Latour, Sylvain [6 ,8 ]
Barlogis, Vincent [9 ]
Galambrun, Claire [10 ,11 ]
Stray-Pedersen, Asbjorg [12 ]
Erichsen, Hans Christian [13 ]
Marsh, Rebecca A. [1 ,2 ]
机构
[1] Cincinnati Childrens Hosp Med Ctr, Div Bone Marrow Transplantat & Immune Deficiency, Cincinnati, OH 45229 USA
[2] Univ Cincinnati, Cincinnati, OH 45221 USA
[3] NIH, Serv Immunol, Dept Lab Med, Clin Ctr, Bldg 10, Bethesda, MD 20892 USA
[4] Japanese Red Cross Nagoya First Hosp, Childrens Med Ctr, Dept Hematol & Oncol, Nagoya, Aichi, Japan
[5] Nagoya Univ, Grad Sch Med, Dept Pediat, Nagoya, Aichi, Japan
[6] INSERM, UMR 1163, Lab Lymphocyte Activat & Susceptibil EBV Infect, Paris, France
[7] Univ Paris Diderot, Hop St Louis, AP HP, Dept Clin Immunol, Paris, France
[8] Univ Paris 05, Sorbonne Paris Cite, Imagine Inst, Paris, France
[9] La Timone Hosp, Dept Pediat Immunol, Marseille, France
[10] Timone Enfants Hosp, Dept Pediat Hematol & Oncol, Marseille, France
[11] Aix Marseille Univ, Marseille, France
[12] Oslo Univ Hosp, Norwegian Natl Unit Newborn Screening, Oslo, Norway
[13] Oslo Univ Hosp, Rigshosp, Sect Specialized Pediat Med, Oslo, Norway
基金
美国国家卫生研究院;
关键词
IKAROS;
D O I
10.1016/j.jaci.2019.03.025
中图分类号
R392 [医学免疫学];
学科分类号
100102 ;
摘要
[No abstract available]
引用
收藏
页码:339 / 342
页数:4
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