Mapping the natural history of Huntington disease

被引:1
作者
Barker, Roger A. [1 ]
Mason, Sarah L. [1 ]
机构
[1] Univ Cambridge, John van Geest Ctr Brain Repair, Dept Clin Neurosci, Cambridge CB2 0PY, England
关键词
D O I
10.1038/nrneurol.2013.253
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
A key challenge to improving the design of clinical trials in Huntington disease (HD) has been the limited data on the natural history of HD. A recent prospective longitudinal study has provided important information in this regard, which could be useful for future translation of disease-modifying therapies for early-stage HD.
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页码:12 / 13
页数:3
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