Effects of Lumacaftor/Ivacaftor in a Pediatric Cohort Homozygous for F508del-CFTR

被引：1
|
作者：
Egan, Marie E. [1 ,2 ]
机构：
[1] Yale Sch Med, Dept Pediat, New Haven, CT 06520 USA
[2] Yale Sch Med, Dept Cellular & Mol Physiol, New Haven, CT 06520 USA
来源：
AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE | 2017年 / 195卷 / 07期
关键词：
CYSTIC-FIBROSIS; PHE508DEL CFTR; IVACAFTOR; MUTATION; TRIAL;
D O I：
10.1164/rccm.201611-2290ED
中图分类号：
R4 [临床医学];
学科分类号：
1002 ; 100602 ;
摘要：
引用
收藏
页码：849 / 850
页数：2
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