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- [21] Design of Crotoxin-Based Peptides with Potentiator Activity Targeting the D-F508NBD1 Cystic Fibrosis Transmem- brane Conductance RegulatorJOURNAL OF MOLECULAR BIOLOGY, 2023, 435 (03)Ravatin, Marc论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, France Sanofi, R&D, Integrated Drug Discovery, In Vitro Biol, Vitry sur Seine, France Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceOdolczyk, Norbert论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, France Univ Warsaw, Inst Expt Plant Biol & Biotechnol, Dept Syst Biol, Miecznikowa 1, PL-02096 Warsaw, Poland Polish Acad Sci, Inst Biochem & Biophys, Pawinskiego 5a, PL-02106 Warsaw, Poland Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceServel, Nathalie论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Inst Necker Enfants Malades INEM, INSERM, CNRS,UMR 8253 U1151, 160 rue Vaugirard, F-75015 Paris, France Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceGuijarro, J. Inaki论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Inst Pasteur, Biol NMR & HDX MS Technol Platform, CNRS UMR 3528, 28 rue Dr Roux, F-75015 Paris, France Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceTagat, Eric论文数: 0 引用数: 0 h-index: 0机构: Sanofi, R&D, Integrated Drug Discovery, In Vitro Biol, Vitry sur Seine, France Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceChevalier, Benoit论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Inst Necker Enfants Malades INEM, INSERM, CNRS,UMR 8253 U1151, 160 rue Vaugirard, F-75015 Paris, France Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceBaatallah, Nesrine论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Inst Necker Enfants Malades INEM, INSERM, CNRS,UMR 8253 U1151, 160 rue Vaugirard, F-75015 Paris, France Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceCorringer, Pierre-Jean论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceLukacs, Gergely L.论文数: 0 引用数: 0 h-index: 0机构: McGill Univ, Dept Physiol & Biochem, Montreal, PQ, Canada Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceEdelman, Aleksander论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, France论文数: 引用数: h-index:机构:Chambard, Jean -Marie论文数: 0 引用数: 0 h-index: 0机构: Sanofi, R&D, Integrated Drug Discovery, In Vitro Biol, Vitry sur Seine, France Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceHinzpeter, Alexandre论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Inst Necker Enfants Malades INEM, INSERM, CNRS,UMR 8253 U1151, 160 rue Vaugirard, F-75015 Paris, France Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, FranceFaure, Grazyna论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, France Univ Paris Cite, Inst Pasteur, CNRS UMR 3571, Recepteurs Canaux,Dept Neurosci, 25, rue du Dr Roux, F-75015 Paris, France
- [22] Pharmacological chaperone-rescued cystic fibrosis CFTR-F508del mutant overcomes PRAF2-gated access to endoplasmic reticulum exit sitesCellular and Molecular Life Sciences, 2022, 79Kusumika Saha论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutBenoit Chevalier论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutStéphane Doly论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutNesrine Baatallah论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutThomas Guilbert论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutIwona Pranke论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutMark G. H. Scott论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutHervé Enslen论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutChiara Guerrera论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutCérina Chuon论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutAleksander Edelman论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutIsabelle Sermet-Gaudelus论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutAlexandre Hinzpeter论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,InstitutStefano Marullo论文数: 0 引用数: 0 h-index: 0机构: Université Paris Cité,Institut
- [23] The L467F-F508del Complex Allele Hampers Pharmacological Rescue of Mutant CFTR by Elexacaftor/Tezacaftor/Ivacaftor in Cystic Fibrosis Patients: The Value of the Ex Vivo Nasal Epithelial Model to Address Non-Responders to CFTR-Modulating DrugsINTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2022, 23 (06)Sondo, Elvira论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyCresta, Federico论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOSD Ctr Fibrosi Cist, Ist Giannina Gaslini, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyPastorino, Cristina论文数: 0 引用数: 0 h-index: 0机构: Univ Genoa, Dept Neurosci Rehabil Ophthalmol Genet Maternal &, I-16132 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyTomati, Valeria论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyCapurro, Valeria论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyPesce, Emanuela论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyLena, Mariateresa论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyIacomino, Michele论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyBaffico, Ave Maria论文数: 0 引用数: 0 h-index: 0机构: IRCCS, Ist Giannina Gaslini, UOC Lab Genet Umana, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyCoviello, Domenico论文数: 0 引用数: 0 h-index: 0机构: IRCCS, Ist Giannina Gaslini, UOC Lab Genet Umana, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyBandiera, Tiziano论文数: 0 引用数: 0 h-index: 0机构: Fdn Ist Italiano Tecnol, D3 PharmaChem, I-16163 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyZara, Federico论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, Italy Univ Genoa, Dept Neurosci Rehabil Ophthalmol Genet Maternal &, I-16132 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyGalietta, Luis J., V论文数: 0 引用数: 0 h-index: 0机构: Telethon Inst Genet & Med TIGEM, I-80078 Pozzuoli, Italy Univ Naples Federico II, Dept Translat Med Sci DISMET, I-80131 Naples, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyBocciardi, Renata论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, Italy Univ Genoa, Dept Neurosci Rehabil Ophthalmol Genet Maternal &, I-16132 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyCastellani, Carlo论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOSD Ctr Fibrosi Cist, Ist Giannina Gaslini, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, ItalyPedemonte, Nicoletta论文数: 0 引用数: 0 h-index: 0机构: IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, Italy IRCCS, UOC Genet Med, Ist Giannina Gaslini, I-16147 Genoa, Italy
- [24] Innovative Strategy toward Mutant CFTR Rescue in Cystic Fibrosis: Design and Synthesis of Thiadiazole Inhibitors of the E3 Ligase RNF5JOURNAL OF MEDICINAL CHEMISTRY, 2023, 66 (14) : 9797 - 9822Brusa, Irene论文数: 0 引用数: 0 h-index: 0机构: Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, Italy Ist Italiano Tecnol, Computat & Chem Biol, I-16163 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalySondo, Elvira论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, UOC Genet Med, I-16147 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyPesce, Emanuela论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, UOC Genet Med, I-16147 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyTomati, Valeria论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, UOC Genet Med, I-16147 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyGioia, Dario论文数: 0 引用数: 0 h-index: 0机构: Ist Italiano Tecnol, Computat & Chem Biol, I-16163 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyFalchi, Federico论文数: 0 引用数: 0 h-index: 0机构: Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, Italy Ist Italiano Tecnol, Computat & Chem Biol, I-16163 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyBalboni, Beatrice论文数: 0 引用数: 0 h-index: 0机构: Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, Italy Ist Italiano Tecnol, Computat & Chem Biol, I-16163 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyMartinez, Jose Antonio Ortega论文数: 0 引用数: 0 h-index: 0机构: Ist Italiano Tecnol, Computat & Chem Biol, I-16163 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyVeronesi, Marina论文数: 0 引用数: 0 h-index: 0机构: Ist Italiano Tecnol, Struct Biophys & Translat Pharmacol Facil, I-16163 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyRomeo, Elisa论文数: 0 引用数: 0 h-index: 0机构: Ist Italiano Tecnol, Struct Biophys & Translat Pharmacol Facil, I-16163 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyMargaroli, Natasha论文数: 0 引用数: 0 h-index: 0机构: Ist Italiano Tecnol, Struct Biophys & Translat Pharmacol Facil, I-16163 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, Italy论文数: 引用数: h-index:机构:Girotto, Stefania论文数: 0 引用数: 0 h-index: 0机构: Ist Italiano Tecnol, Struct Biophys & Translat Pharmacol Facil, I-16163 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyPedemonte, Nicoletta论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, UOC Genet Med, I-16147 Genoa, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyRoberti, Marinella论文数: 0 引用数: 0 h-index: 0机构: Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, Italy Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, ItalyCavalli, Andrea论文数: 0 引用数: 0 h-index: 0机构: Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, Italy Ist Italiano Tecnol, Computat & Chem Biol, I-16163 Genoa, Italy EPFL CECAM, Ctr Europeen Calcul Atom & Mol, CH-1015 Lausanne, Switzerland Univ Bologna, Dept Pharm & Biotechnol, I-40126 Bologna, Italy
- [25] Activation of 3-Phosphoinositide-dependent Kinase 1 (PDK1) and Serum-and Glucocorticoid-induced Protein Kinase 1 (SGK1) by Short-chain Sphingolipid C4-ceramide Rescues the Trafficking Defect of ΔF508-Cystic Fibrosis Transmembrane Conductance Regulator (ΔF508-CFTR)JOURNAL OF BIOLOGICAL CHEMISTRY, 2014, 289 (52) : 35953 - 35968Caohuy, Hung论文数: 0 引用数: 0 h-index: 0机构: Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USA Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USAYang, Qingfeng论文数: 0 引用数: 0 h-index: 0机构: Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USA Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USAEudy, Yvonne论文数: 0 引用数: 0 h-index: 0机构: Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USA Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USAHa, Thien-An论文数: 0 引用数: 0 h-index: 0机构: Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USA Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USAXu, Andrew E.论文数: 0 引用数: 0 h-index: 0机构: Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USA Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USAGlover, Matthew论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Sch Med, Dept Cell Biol, Pittsburgh, PA 15224 USA Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USAFrizzell, Raymond A.论文数: 0 引用数: 0 h-index: 0机构: Univ Pittsburgh, Sch Med, Dept Cell Biol, Pittsburgh, PA 15224 USA Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USAJozwik, Catherine论文数: 0 引用数: 0 h-index: 0机构: Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USA Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USAPollard, Harvey B.论文数: 0 引用数: 0 h-index: 0机构: Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USA Uniformed Serv Univ Hlth Sci, Sch Med, Dept Anat Physiol & Genet, Bethesda, MD 20814 USA
- [26] Reduced expression of Tis7/IFRD1 protein in murine and human cystic fibrosis airway epithelial cell models homozygous for the F508del-CFTR mutationBIOCHEMICAL AND BIOPHYSICAL RESEARCH COMMUNICATIONS, 2011, 411 (03) : 471 - 476Blanchard, Elise论文数: 0 引用数: 0 h-index: 0机构: INSERM, Cdr St Antoine, UMR S U 938, F-75012 Paris, France Univ Paris 06, F-75006 Paris, France INSERM, Cdr St Antoine, UMR S U 938, F-75012 Paris, FranceMarie, Solenne论文数: 0 引用数: 0 h-index: 0机构: INSERM, Cdr St Antoine, UMR S U 938, F-75012 Paris, France Univ Paris 06, F-75006 Paris, France INSERM, Cdr St Antoine, UMR S U 938, F-75012 Paris, France论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Tabary, Olivier论文数: 0 引用数: 0 h-index: 0机构: INSERM, Cdr St Antoine, UMR S U 938, F-75012 Paris, France Univ Paris 06, F-75006 Paris, France INSERM, Cdr St Antoine, UMR S U 938, F-75012 Paris, FranceClement, Annick论文数: 0 引用数: 0 h-index: 0机构: INSERM, Cdr St Antoine, UMR S U 938, F-75012 Paris, France Univ Paris 06, F-75006 Paris, France Hop Trousseau, AP HP, Pediat Pulm Dept, F-75012 Paris, France INSERM, Cdr St Antoine, UMR S U 938, F-75012 Paris, FranceJacquot, Jacky论文数: 0 引用数: 0 h-index: 0机构: INSERM, Cdr St Antoine, UMR S U 938, F-75012 Paris, France Univ Paris 06, F-75006 Paris, France INSERM, Cdr St Antoine, UMR S U 938, F-75012 Paris, France