Defibrotide (DF) in the Treatment of Severe Hepatic Veno-Occlusive Disease (VOD) with Multi-Organ Failure (MOF) Following Stem Cell Transplantation (SCT): Results of a Phase 3 Study Utilizing a Historical Control

被引:1
作者
Richardson, Paul [1 ]
Tomblyn, Marcie [2 ]
Kernan, Nancy [3 ]
Brochstein, Joel A. [4 ]
Mineishi, Shin [5 ]
Termuhlen, Amanda [6 ]
Arai, Sally [7 ]
Grupp, Stephan A. [8 ,9 ]
Guinan, Eva [1 ]
Martin, Paul L. [10 ]
Corbacioglu, Selim [11 ]
Holler, Ernst [12 ]
D'Agostino, Ralph [13 ]
Massaro, Joseph [13 ]
Hannah, Alison L. [14 ]
Iacobelli, Massimo [14 ]
Soiffer, Robert J. [1 ]
机构
[1] Dana Farber Canc Inst, Boston, MA 02115 USA
[2] Univ S Florida, H Lee Moffitt Canc Ctr, Tampa, FL 33682 USA
[3] Mem Sloan Kettering Canc Ctr, New York, NY 10021 USA
[4] Hackensack Univ, Med Ctr, Hackensack, NJ USA
[5] Univ Michigan, Ann Arbor, MI 48109 USA
[6] Nationwide Childrens Hosp, Dept Pediat Hem Oncol, Columbus, OH USA
[7] Stanford Univ, Med Ctr, Stanford, CA 94305 USA
[8] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
[9] Univ Penn, Sch Med, Philadelphia, PA 19104 USA
[10] Duke Univ, Med Ctr, Durham, NC USA
[11] Univ Ulm, Dept Pediat, D-7900 Ulm, Germany
[12] Klinikum Univ Regensburg, Abt Hamatol Intern Onkol, Regensburg, Germany
[13] Boston Univ, Boston, MA 02215 USA
[14] Gentium Pharmaceut SPA, Villa Guardia, Italy
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中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
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页码:272 / 273
页数:2
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