Allele-Specific Gene Editing for the Treatment of Autosomal Dominant Retinitis Pigmentosa

被引：0

作者：

Liau, Gene ^{[1
]}

Rao, Kollu N. ^{[2
]}

Bartsevich, Victor V. ^{[1
]}

Smith, Jeff ^{[1
]}

Jantz, Darek ^{[1
]}

Hirsch, Matthew ^{[2
]}

机构：

[1] Precis BioSci, Gene Therapy, Durham, NC USA

[2] Univ N Carolina, Dept Ophthalmol, Gene Therapy Ctr, Chapel Hill, NC USA

来源：

MOLECULAR THERAPY | 2017年 / 25卷 / 05期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

762

引用

页码：352 / 352

页数：1

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