Allele-Specific Gene Editing for the Treatment of Autosomal Dominant Retinitis Pigmentosa

被引:0
|
作者
Liau, Gene [1 ]
Rao, Kollu N. [2 ]
Bartsevich, Victor V. [1 ]
Smith, Jeff [1 ]
Jantz, Darek [1 ]
Hirsch, Matthew [2 ]
机构
[1] Precis BioSci, Gene Therapy, Durham, NC USA
[2] Univ N Carolina, Dept Ophthalmol, Gene Therapy Ctr, Chapel Hill, NC USA
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D O I
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中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
762
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页码:352 / 352
页数:1
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