A response to Germain, et al. The effect of enzyme replacement therapy on clinical outcomes in male patients with Fabry disease: A systematic literature review by a European panel of experts. Mol Genet Metab Rep Feb 6 2019

被引：2

作者：

Gurevich, Andrey ^{[1
]}

Schenk, Jorn ^{[1
]}

Wellhoefer, Hartmann ^{[1
]}

Kalampoki, Vasiliki ^{[1
]}

机构：

[1] Shire, Zug, Switzerland

来源：

关键词：

D O I：

10.1016/j.ymgmr.2019.100471

中图分类号：

Q3 [遗传学];

学科分类号：

071007 ; 090102 ;

摘要：

引用

页数：1

共 2 条

Germain, Dominique P. ;

Elliott, Perry M. ;

Falissard, Bruno ;

Fomin, Victor V. ;

Hilz, Max J. ;

Jovanovic, Ana ;

Kantola, Ilkka ;

Linhart, Ales ;

Mignani, Renzo ;

Namdar, Mehdi ;

Nowak, Albina ;

Oliveira, Joao-Paulo ;

Pieroni, Maurizio ;

Viana-Baptista, Miguel ;

Wanner, Christoph ;

Spada, Marco .

[2]

Liberati A, 2009, PLOS MED, V6, DOI [10.1371/journal.pmed.1000100, 10.7326/0003-4819-151-4-200908180-00136]