Intestinal organoids to model cystic fibrosis

被引:37
作者
van Mourik, Peter [1 ]
Beekman, Jeffrey M. [1 ,2 ]
van der Ent, Cornelis K. [1 ]
机构
[1] Univ Utrecht, Univ Med Ctr Utrecht, Wilhelmina Childrens Hosp, Dept Pediat Pulmonol, Utrecht, Netherlands
[2] Univ Utrecht, Univ Med Ctr Utrecht, Regenerat Med Ctr Utrecht, Utrecht, Netherlands
基金
欧盟地平线“2020”;
关键词
HUMAN COLON; CFTR; DISEASE; G551D; POTENTIATOR; ION;
D O I
10.1183/13993003.02379-2018
中图分类号
R56 [呼吸系及胸部疾病];
学科分类号
摘要
[No abstract available]
引用
收藏
页数:6
相关论文
共 38 条
[1]  
[Anonymous], 2016, Pediatr Pulmonol, V51, pS194, DOI 10.1002/ppul.23576
[2]   R560S: A class II CFTR mutation that is not rescued by current modulators [J].
Awatade, Nikhil T. ;
Ramalho, Sofia ;
Silva, Iris A. L. ;
Felicio, Vernica ;
Botelho, Hugo M. ;
de Poel, Eyleen ;
Vonk, Annelotte ;
Beekman, Jeffrey M. ;
Farinha, Carlos M. ;
Amaral, Margarida D. .
JOURNAL OF CYSTIC FIBROSIS, 2019, 18 (02) :182-189
[3]   Rectal Organoids Enable Personalized Treatment of Cystic Fibrosis [J].
Berkers, Gitte ;
van Mourik, Peter ;
Vonk, Annelotte M. ;
Kruisselbrink, Evelien ;
Dekkers, Johanna F. ;
de Winter-de Groot, Karin M. ;
Arets, Hubertus G. M. ;
Marck-van der Wilt, Rozemarijn E. P. ;
Dijkema, Jasper S. ;
Vanderschuren, Maaike M. ;
Houwen, Roderick H. J. ;
Heijerman, Harry G. M. ;
van de Graaf, Eduard A. ;
Elias, Sjoerd G. ;
Majoor, Christof J. ;
Koppelman, Gerard H. ;
Roukema, Jolt ;
Bakker, Marleen ;
Janssens, Hettie M. ;
van der Meer, Renske ;
Vries, Robert G. J. ;
Clevers, Hans C. ;
de Jonge, Hugo R. ;
Beekman, Jeffrey M. ;
van der Ent, Cornelis K. .
CELL REPORTS, 2019, 26 (07) :1701-+
[4]   Forskolin-induced Swelling in Intestinal Organoids: An In Vitro Assay for Assessing Drug Response in Cystic Fibrosis Patients [J].
Boj, Sylvia F. ;
Vonk, Annelotte M. ;
Statia, Marvin ;
Su, Jinyi ;
Vries, Robert R. G. ;
Beekman, Jeffrey M. ;
Clevers, Hans .
JOVE-JOURNAL OF VISUALIZED EXPERIMENTS, 2017, (120)
[5]   Brushed nasal epithelial cells are a surrogate for bronchial epithelial CFTR studies [J].
Brewington, John J. ;
Filbrandt, Erin T. ;
LaRosa, F. J., III ;
Moncivaiz, Jessica D. ;
Ostmann, Alicia J. ;
Strecker, Lauren M. ;
Clancy, John P. .
JCI INSIGHT, 2018, 3 (13)
[6]   The effect of premature termination codon mutations on CFTR mRNA abundance in human nasal epithelium and intestinal organoids: a basis for read-through therapies in cystic fibrosis [J].
Clarke, Luka A. ;
Awatade, Nikhil T. ;
Felicio, Veronica M. ;
Silva, Iris A. ;
Calucho, Maite ;
Pereira, Luisa ;
Azevedo, Pilar ;
Cavaco, Jose ;
Barreto, Celeste ;
Bertuzzo, Carmen ;
Gartner, Silvia ;
Beekman, Jeffrey ;
Amaral, Margarida D. .
HUMAN MUTATION, 2019, 40 (03) :326-334
[7]   Modeling Development and Disease with Organoids [J].
Clevers, Hans .
CELL, 2016, 165 (07) :1586-1597
[8]   CFTR biomarkers: time for promotion to surrogate end-point? [J].
De Boeck, K. ;
Kent, L. ;
Davies, J. ;
Derichs, N. ;
Amaral, M. ;
Rowe, S. M. ;
Middleton, P. ;
de Jonge, H. ;
Bronsveld, I. ;
Wilschanski, M. ;
Melotti, P. ;
Danner-Boucher, I. ;
Boerner, S. ;
Fajac, I. ;
Southern, K. ;
de Nooijer, R. A. ;
Bot, A. ;
de Rijke, Y. ;
de Wachter, E. ;
Leal, T. ;
Vermeulen, F. ;
Hug, M. J. ;
Rault, G. ;
Nguyen-Khoa, T. ;
Barreto, C. ;
Proesmans, M. ;
Sermet-Gaudelus, I. .
EUROPEAN RESPIRATORY JOURNAL, 2013, 41 (01) :203-216
[9]   Stratifying infants with cystic fibrosis for disease severity using intestinal organoid swelling as a biomarker of CFTR function [J].
de Winter-de Groot, Karin M. ;
Janssens, Hettie M. ;
van Uum, Rick T. ;
Dekkers, Johanna F. ;
Berkers, Gitte ;
Vonk, Annelotte ;
Kruisselbrink, Evelien ;
Oppelaar, Hugo ;
Vries, Robert ;
Clevers, Hans ;
Houwen, Roderick H. J. ;
Escher, Johanna C. ;
Elias, Sjoerd G. ;
de Jonge, Hugo R. ;
de Rijke, Yolanda B. ;
Tiddens, Harm A. W. M. ;
van der Ent, Cornelis K. ;
Beekman, Jeffrey M. .
EUROPEAN RESPIRATORY JOURNAL, 2018, 52 (03)
[10]   Potentiator synergy in rectal organoids carrying S1251N, G551D, or F508de1 CFTR mutations [J].
Dekkers, Johanna F. ;
Van Mourik, Peter ;
Vonk, Annelotte M. ;
Kruisselbrink, Evelien ;
Berkers, Gitte ;
de Winter-de Groot, Karin M. ;
Janssens, Hettie M. ;
Bronsveld, Inez ;
van der Ent, Cornelis K. ;
de Jonge, Hugo R. ;
Beekman, Jeffrey M. .
JOURNAL OF CYSTIC FIBROSIS, 2016, 15 (05) :568-578