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Bringing gene therapy to the clinic
被引:2
作者
:
Ball, BG
论文数:
0
引用数:
0
h-index:
0
机构:
Univ So Calif, Keck Sch Med, Gene Therapy Labs, Los Angeles, CA 90089 USA
Univ So Calif, Keck Sch Med, Gene Therapy Labs, Los Angeles, CA 90089 USA
Ball, BG
[
1
]
Anderson, WF
论文数:
0
引用数:
0
h-index:
0
机构:
Univ So Calif, Keck Sch Med, Gene Therapy Labs, Los Angeles, CA 90089 USA
Univ So Calif, Keck Sch Med, Gene Therapy Labs, Los Angeles, CA 90089 USA
Anderson, WF
[
1
]
机构
:
[1]
Univ So Calif, Keck Sch Med, Gene Therapy Labs, Los Angeles, CA 90089 USA
来源
:
JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION
|
2000年
/ 284卷
/ 21期
关键词
:
D O I
:
10.1001/jama.284.21.2788
中图分类号
:
R5 [内科学];
学科分类号
:
1002 ;
100201 ;
摘要
:
引用
收藏
页码:2788 / 2788
页数:1
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Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
[J].
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LACK OF EXPRESSION FROM A RETROVIRAL VECTOR AFTER TRANSDUCTION OF MURINE HEMATOPOIETIC STEM-CELLS IS ASSOCIATED WITH METHYLATION IN-VIVO
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←
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共 5 条
[1]
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease
[J].
Cavazzana-Calvo, M
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Cavazzana-Calvo, M
;
Hacein-Bey, S
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0
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0
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Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Hacein-Bey, S
;
Basile, CD
论文数:
0
引用数:
0
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Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Basile, CD
;
Gross, F
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0
引用数:
0
h-index:
0
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Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Gross, F
;
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论文数:
0
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Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Yvon, E
;
Nusbaum, P
论文数:
0
引用数:
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h-index:
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机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Nusbaum, P
;
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0
引用数:
0
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Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Selz, F
;
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论文数:
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h-index:
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论文数:
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0
h-index:
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0
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Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Casanova, JL
;
论文数:
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h-index:
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Bousso, P
;
Le Deist, F
论文数:
0
引用数:
0
h-index:
0
机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Le Deist, F
;
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论文数:
0
引用数:
0
h-index:
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机构:
Hop Necker Enfants Malad, INSERM, U429, F-75743 Paris 15, France
Fischer, A
.
SCIENCE,
2000,
288
(5466)
:669
-672
[2]
LACK OF EXPRESSION FROM A RETROVIRAL VECTOR AFTER TRANSDUCTION OF MURINE HEMATOPOIETIC STEM-CELLS IS ASSOCIATED WITH METHYLATION IN-VIVO
[J].
CHALLITA, PM
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP LOS ANGELES,DIV RES IMMUNOL BONE MARROW TRANSPLANTAT,4650 SUNSET BLVD,LOS ANGELES,CA 90027
CHALLITA, PM
;
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论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP LOS ANGELES,DIV RES IMMUNOL BONE MARROW TRANSPLANTAT,4650 SUNSET BLVD,LOS ANGELES,CA 90027
KOHN, DB
.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
1994,
91
(07)
:2567
-2571
[3]
Therapeutic haemoglobin synthesis in β-thalassaemic mice expressing lentivirus-encoded human β-globin
[J].
May, C
论文数:
0
引用数:
0
h-index:
0
机构:
Mem Sloan Kettering Canc Ctr, Dept Human Genet, New York, NY 10021 USA
May, C
;
Rivella, S
论文数:
0
引用数:
0
h-index:
0
机构:
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Rivella, S
;
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论文数:
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h-index:
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机构:
Mem Sloan Kettering Canc Ctr, Dept Human Genet, New York, NY 10021 USA
Callegari, J
;
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论文数:
0
引用数:
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h-index:
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机构:
Mem Sloan Kettering Canc Ctr, Dept Human Genet, New York, NY 10021 USA
Heller, G
;
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论文数:
0
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h-index:
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;
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论文数:
0
引用数:
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h-index:
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机构:
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Luzzatto, L
;
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论文数:
0
引用数:
0
h-index:
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机构:
Mem Sloan Kettering Canc Ctr, Dept Human Genet, New York, NY 10021 USA
Sadelain, M
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NATURE,
2000,
406
(6791)
:82
-86
[4]
SAFETY CONSIDERATIONS IN SOMATIC GENE-THERAPY OF HUMAN-DISEASE WITH RETROVIRUS VECTORS
[J].
TEMIN, HM
论文数:
0
引用数:
0
h-index:
0
机构:
McArdle Laboratory, University of Wisconsin, Madison
TEMIN, HM
.
HUMAN GENE THERAPY,
1990,
1
(02)
:111
-123
[5]
2000, HUMAN GENE THER, V11, P1745
←
1
→