共 9 条
[1]
Effect of VX-770 in Persons with Cystic Fibrosis and the G551D-CFTR Mutation
[J].
Accurso, Frank J.
;
Rowe, Steven M.
;
Clancy, J. P.
;
Boyle, Michael P.
;
Dunitz, Jordan M.
;
Durie, Peter R.
;
Sagel, Scott D.
;
Hornick, Douglas B.
;
Konstan, Michael W.
;
Donaldson, Scott H.
;
Moss, Richard B.
;
Pilewski, Joseph M.
;
Rubenstein, Ronald C.
;
Uluer, Ahmet Z.
;
Aitken, Moira L.
;
Freedman, Steven D.
;
Rose, Lynn M.
;
Mayer-Hamblett, Nicole
;
Dong, Qunming
;
Zha, Jiuhong
;
Stone, Anne J.
;
Olson, Eric R.
;
Ordonez, Claudia L.
;
Campbell, Preston W.
;
Ashlock, Melissa A.
;
Ramsey, Bonnie W.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2010, 363 (21)
:1991-2003

Accurso, Frank J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Colorado Denver, Aurora, CO 80045 USA
Childrens Hosp, Aurora, CO USA Univ Colorado Denver, Aurora, CO 80045 USA

Rowe, Steven M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Birmingham, AL USA Univ Colorado Denver, Aurora, CO 80045 USA

Clancy, J. P.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Birmingham, AL USA Univ Colorado Denver, Aurora, CO 80045 USA

Boyle, Michael P.
论文数: 0 引用数: 0
h-index: 0
机构:
Johns Hopkins Med Inst, Baltimore, MD 21205 USA Univ Colorado Denver, Aurora, CO 80045 USA

Dunitz, Jordan M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Minnesota, Minneapolis, MN USA Univ Colorado Denver, Aurora, CO 80045 USA

Durie, Peter R.
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp Sick Children, Toronto, ON M5G 1X8, Canada
Univ Toronto, Toronto, ON, Canada Univ Colorado Denver, Aurora, CO 80045 USA

Sagel, Scott D.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Colorado Denver, Aurora, CO 80045 USA
Childrens Hosp, Aurora, CO USA Univ Colorado Denver, Aurora, CO 80045 USA

Hornick, Douglas B.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Iowa, Carver Coll Med, Iowa City, IA USA Univ Colorado Denver, Aurora, CO 80045 USA

Konstan, Michael W.
论文数: 0 引用数: 0
h-index: 0
机构:
Rainbow Babies & Childrens Hosp, Cleveland, OH 44106 USA
Case Western Reserve Univ, Sch Med, Cleveland, OH USA Univ Colorado Denver, Aurora, CO 80045 USA

Donaldson, Scott H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ N Carolina, Chapel Hill, NC USA Univ Colorado Denver, Aurora, CO 80045 USA

Moss, Richard B.
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Sch Med, Palo Alto, CA 94304 USA Univ Colorado Denver, Aurora, CO 80045 USA

Pilewski, Joseph M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Pittsburgh, Pittsburgh, PA USA Univ Colorado Denver, Aurora, CO 80045 USA

Rubenstein, Ronald C.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
Univ Penn, Sch Med, Philadelphia, PA 19104 USA Univ Colorado Denver, Aurora, CO 80045 USA

Uluer, Ahmet Z.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, Boston, MA 02115 USA Univ Colorado Denver, Aurora, CO 80045 USA

Aitken, Moira L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Seattle, WA 98195 USA Univ Colorado Denver, Aurora, CO 80045 USA

Freedman, Steven D.
论文数: 0 引用数: 0
h-index: 0
机构:
Beth Israel Deaconess Med Ctr, Boston, MA 02215 USA Univ Colorado Denver, Aurora, CO 80045 USA

Rose, Lynn M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Seattle, WA 98195 USA
Seattle Childrens Hosp, Seattle, WA USA Univ Colorado Denver, Aurora, CO 80045 USA

Mayer-Hamblett, Nicole
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Seattle, WA 98195 USA
Seattle Childrens Hosp, Seattle, WA USA Univ Colorado Denver, Aurora, CO 80045 USA

Dong, Qunming
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Colorado Denver, Aurora, CO 80045 USA

Zha, Jiuhong
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Colorado Denver, Aurora, CO 80045 USA

Stone, Anne J.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Colorado Denver, Aurora, CO 80045 USA

Olson, Eric R.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Colorado Denver, Aurora, CO 80045 USA

Ordonez, Claudia L.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Colorado Denver, Aurora, CO 80045 USA

Campbell, Preston W.
论文数: 0 引用数: 0
h-index: 0
机构:
Cyst Fibrosis Fdn Therapeut, Bethesda, MD USA Univ Colorado Denver, Aurora, CO 80045 USA

Ashlock, Melissa A.
论文数: 0 引用数: 0
h-index: 0
机构:
Cyst Fibrosis Fdn Therapeut, Bethesda, MD USA Univ Colorado Denver, Aurora, CO 80045 USA

Ramsey, Bonnie W.
论文数: 0 引用数: 0
h-index: 0
机构:
Seattle Childrens Hosp, Seattle, WA USA Univ Colorado Denver, Aurora, CO 80045 USA
[2]
DEFECTIVE INTRACELLULAR-TRANSPORT AND PROCESSING OF CFTR IS THE MOLECULAR-BASIS OF MOST CYSTIC-FIBROSIS
[J].
CHENG, SH
;
GREGORY, RJ
;
MARSHALL, J
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PAUL, S
;
SOUZA, DW
;
WHITE, GA
;
ORIORDAN, CR
;
SMITH, AE
.
CELL,
1990, 63 (04)
:827-834

CHENG, SH
论文数: 0 引用数: 0
h-index: 0
机构: Genzyme Corporation, Framingham

GREGORY, RJ
论文数: 0 引用数: 0
h-index: 0
机构: Genzyme Corporation, Framingham

MARSHALL, J
论文数: 0 引用数: 0
h-index: 0
机构: Genzyme Corporation, Framingham

PAUL, S
论文数: 0 引用数: 0
h-index: 0
机构: Genzyme Corporation, Framingham

SOUZA, DW
论文数: 0 引用数: 0
h-index: 0
机构: Genzyme Corporation, Framingham

WHITE, GA
论文数: 0 引用数: 0
h-index: 0
机构: Genzyme Corporation, Framingham

ORIORDAN, CR
论文数: 0 引用数: 0
h-index: 0
机构: Genzyme Corporation, Framingham

SMITH, AE
论文数: 0 引用数: 0
h-index: 0
机构: Genzyme Corporation, Framingham
[3]
State of the Art: Why do the lungs of patients with cystic fibrosis become infected and why can't they clear the infection?
[J].
Chmiel, JF
;
Davis, PB
.
RESPIRATORY RESEARCH,
2003, 4 (08)

Chmiel, JF
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Rainbow Babies & Childrens Hosp, Sch Med, Dept Pediat, Cleveland, OH 44106 USA Case Western Reserve Univ, Rainbow Babies & Childrens Hosp, Sch Med, Dept Pediat, Cleveland, OH 44106 USA

Davis, PB
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Rainbow Babies & Childrens Hosp, Sch Med, Dept Pediat, Cleveland, OH 44106 USA Case Western Reserve Univ, Rainbow Babies & Childrens Hosp, Sch Med, Dept Pediat, Cleveland, OH 44106 USA
[4]
Genetic modifiers of lung disease in cystic fibrosis
[J].
Drumm, ML
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Konstan, MW
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Schluchter, MD
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Handler, A
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Pace, R
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Zou, F
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Zariwala, M
;
Fargo, D
;
Xu, AR
;
Dunn, JM
;
Darrah, RJ
;
Dorfman, R
;
Sandford, AJ
;
Corey, M
;
Zielenski, J
;
Durie, P
;
Goddard, K
;
Yankaskas, JR
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Wright, FA
;
Knowles, MR
.
NEW ENGLAND JOURNAL OF MEDICINE,
2005, 353 (14)
:1443-1453

Drumm, ML
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Konstan, MW
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Schluchter, MD
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Handler, A
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Pace, R
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Zou, F
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Zariwala, M
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Fargo, D
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Xu, AR
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Dunn, JM
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Darrah, RJ
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Dorfman, R
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Sandford, AJ
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Corey, M
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Zielenski, J
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Durie, P
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Goddard, K
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Yankaskas, JR
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Wright, FA
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA

Knowles, MR
论文数: 0 引用数: 0
h-index: 0
机构: Univ N Carolina, Sch Med, Cyst Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27599 USA
[5]
Thiazolidinone CFTR inhibitor identified by high-throughput screening blocks cholera toxin-induced intestinal fluid secretion
[J].
Ma, TH
;
Thiagarajah, JR
;
Yang, H
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Sonawane, ND
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Folli, C
;
Galietta, LJV
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Verkman, AS
.
JOURNAL OF CLINICAL INVESTIGATION,
2002, 110 (11)
:1651-1658

Ma, TH
论文数: 0 引用数: 0
h-index: 0
机构: Univ Calif San Francisco, Cardiovasc Res Inst, Dept Med, San Francisco, CA 94143 USA

Thiagarajah, JR
论文数: 0 引用数: 0
h-index: 0
机构: Univ Calif San Francisco, Cardiovasc Res Inst, Dept Med, San Francisco, CA 94143 USA

Yang, H
论文数: 0 引用数: 0
h-index: 0
机构: Univ Calif San Francisco, Cardiovasc Res Inst, Dept Med, San Francisco, CA 94143 USA

Sonawane, ND
论文数: 0 引用数: 0
h-index: 0
机构: Univ Calif San Francisco, Cardiovasc Res Inst, Dept Med, San Francisco, CA 94143 USA

Folli, C
论文数: 0 引用数: 0
h-index: 0
机构: Univ Calif San Francisco, Cardiovasc Res Inst, Dept Med, San Francisco, CA 94143 USA

Galietta, LJV
论文数: 0 引用数: 0
h-index: 0
机构: Univ Calif San Francisco, Cardiovasc Res Inst, Dept Med, San Francisco, CA 94143 USA

Verkman, AS
论文数: 0 引用数: 0
h-index: 0
机构: Univ Calif San Francisco, Cardiovasc Res Inst, Dept Med, San Francisco, CA 94143 USA
[6]
Peripheral Protein Quality Control Removes Unfolded CFTR from the Plasma Membrane
[J].
Okiyoneda, Tsukasa
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Barriere, Herve
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Bagdany, Miklos
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Rabeh, Wael M.
;
Du, Kai
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Hoehfeld, Joerg
;
Young, Jason C.
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Lukacs, Gergely L.
.
SCIENCE,
2010, 329 (5993)
:805-810

Okiyoneda, Tsukasa
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada
McGill Univ, GRASP, Montreal, PQ H3G 1Y6, Canada McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada

Barriere, Herve
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada
McGill Univ, GRASP, Montreal, PQ H3G 1Y6, Canada McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada

Bagdany, Miklos
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada
McGill Univ, GRASP, Montreal, PQ H3G 1Y6, Canada McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada

Rabeh, Wael M.
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada
McGill Univ, GRASP, Montreal, PQ H3G 1Y6, Canada McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada

Du, Kai
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada
McGill Univ, GRASP, Montreal, PQ H3G 1Y6, Canada McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada

Hoehfeld, Joerg
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Bonn, Inst Cell Biol, D-53121 Bonn, Germany McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada

Young, Jason C.
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, GRASP, Montreal, PQ H3G 1Y6, Canada
McGill Univ, Dept Chem, Montreal, PQ H3G 1Y6, Canada McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada

Lukacs, Gergely L.
论文数: 0 引用数: 0
h-index: 0
机构:
McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada
McGill Univ, GRASP, Montreal, PQ H3G 1Y6, Canada McGill Univ, Dept Physiol, Montreal, PQ H3G 1Y6, Canada
[7]
A CFTR Potentiator in Patients with Cystic Fibrosis and the G551D Mutation
[J].
Ramsey, Bonnie W.
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Davies, Jane
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McElvaney, N. Gerard
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Tullis, Elizabeth
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Bell, Scott C.
;
Drevinek, Pavel
;
Griese, Matthias
;
McKone, Edward F.
;
Wainwright, Claire E.
;
Konstan, Michael W.
;
Moss, Richard
;
Ratjen, Felix
;
Sermet-Gaudelus, Isabelle
;
Rowe, Steven M.
;
Dong, Qunming
;
Rodriguez, Sally
;
Yen, Karl
;
Ordonez, Claudia
;
Elborn, J. Stuart
.
NEW ENGLAND JOURNAL OF MEDICINE,
2011, 365 (18)
:1663-1672

Ramsey, Bonnie W.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Washington, Dept Pediat, Seattle, WA 98105 USA
Seattle Childrens Hosp, Seattle, WA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Davies, Jane
论文数: 0 引用数: 0
h-index: 0
机构:
Royal Brompton & Harefield Natl Hlth Serv Fdn Tru, Res Biomed Res Unit, London, England Univ Washington, Dept Pediat, Seattle, WA 98105 USA

McElvaney, N. Gerard
论文数: 0 引用数: 0
h-index: 0
机构:
Beaumont Hosp, Royal Coll Surg Ireland, Beaumont, TX USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Tullis, Elizabeth
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Toronto, St Michaels Hosp, Toronto, ON M5B 1W8, Canada Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Bell, Scott C.
论文数: 0 引用数: 0
h-index: 0
机构:
Prince Charles Hosp, Dept Thorac Med, Brisbane, Qld 4032, Australia
Univ Queensland, Queensland Childrens Med Res Inst, Brisbane, Qld, Australia Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Drevinek, Pavel
论文数: 0 引用数: 0
h-index: 0
机构:
Charles Univ Prague, Dept Pediat, Sch Med 2, Prague, Czech Republic Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Griese, Matthias
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Munich, Dr Von Haunerschen Kinderspital, D-80337 Munich, Germany Univ Washington, Dept Pediat, Seattle, WA 98105 USA

McKone, Edward F.
论文数: 0 引用数: 0
h-index: 0
机构:
St Vincents Univ Hosp, Dublin 4, Ireland Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Wainwright, Claire E.
论文数: 0 引用数: 0
h-index: 0
机构:
St Vincents Univ Hosp, Dublin 4, Ireland
Univ Queensland, Queensland Childrens Med Res Inst, Brisbane, Qld, Australia Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Konstan, Michael W.
论文数: 0 引用数: 0
h-index: 0
机构:
Case Western Reserve Univ, Sch Med, Rainbow Babies & Childrens Hosp, Cleveland, OH USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Moss, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Sch Med, Stanford, CA 94305 USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Ratjen, Felix
论文数: 0 引用数: 0
h-index: 0
机构:
Hosp Sick Children, Dept Pediat, Toronto, ON M5G 1X8, Canada Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Sermet-Gaudelus, Isabelle
论文数: 0 引用数: 0
h-index: 0
机构:
Hop Necker Enfants Malad, Ctr Invest Clin, Paris, France Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Rowe, Steven M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Alabama Birmingham, Birmingham, AL USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Dong, Qunming
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Rodriguez, Sally
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Yen, Karl
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Ordonez, Claudia
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut, Cambridge, MA USA Univ Washington, Dept Pediat, Seattle, WA 98105 USA

Elborn, J. Stuart
论文数: 0 引用数: 0
h-index: 0
机构:
Queens Univ Belfast, Ctr Infect & Immun, Belfast, Antrim, North Ireland Univ Washington, Dept Pediat, Seattle, WA 98105 USA
[8]
IDENTIFICATION OF THE CYSTIC-FIBROSIS GENE - CHROMOSOME WALKING AND JUMPING
[J].
ROMMENS, JM
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IANNUZZI, MC
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KEREM, BS
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DRUMM, ML
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MELMER, G
;
DEAN, M
;
ROZMAHEL, R
;
COLE, JL
;
KENNEDY, D
;
HIDAKA, N
;
ZSIGA, M
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BUCHWALD, M
;
RIORDAN, JR
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TSUI, LC
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COLLINS, FS
.
SCIENCE,
1989, 245 (4922)
:1059-1065

ROMMENS, JM
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

IANNUZZI, MC
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

KEREM, BS
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

DRUMM, ML
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

MELMER, G
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

DEAN, M
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

ROZMAHEL, R
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

COLE, JL
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

KENNEDY, D
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

HIDAKA, N
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

ZSIGA, M
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

BUCHWALD, M
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

RIORDAN, JR
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

TSUI, LC
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109

COLLINS, FS
论文数: 0 引用数: 0
h-index: 0
机构: UNIV MICHIGAN,HOWARD HUGHES MED INST,ANN ARBOR,MI 48109
[9]
Rescue of CF airway epithelial cell function in vitro by a CFTR potentiator, VX-770
[J].
Van Goor, Fredrick
;
Hadida, Sabine
;
Grootenhuis, Peter D. J.
;
Burton, Bill
;
Cao, Dong
;
Neuberger, Tim
;
Turnbull, Amanda
;
Singh, Ashvani
;
Joubran, John
;
Hazlewood, Anna
;
Zhou, Jinglan
;
McCartney, Jason
;
Arumugam, Vijayalaksmi
;
Decker, Caroline
;
Yang, Jennifer
;
Young, Chris
;
Olson, Eric R.
;
Wine, Jeffery J.
;
Frizzell, Raymond A.
;
Ashlock, Melissa
;
Negulescu, Paul
.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
2009, 106 (44)
:18825-18830

Van Goor, Fredrick
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Hadida, Sabine
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Grootenhuis, Peter D. J.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Burton, Bill
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Cao, Dong
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Neuberger, Tim
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Turnbull, Amanda
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Singh, Ashvani
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Joubran, John
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Hazlewood, Anna
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Zhou, Jinglan
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

McCartney, Jason
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Arumugam, Vijayalaksmi
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Decker, Caroline
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Yang, Jennifer
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Young, Chris
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Olson, Eric R.
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, Cambridge, MA 02139 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Wine, Jeffery J.
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Univ, Dept Psychol, Cyst Fibrosis Res Lab, Stanford, CA 94305 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Frizzell, Raymond A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Pittsburgh, Sch Med, Dept Cell Biol & Physiol, Pittsburgh, PA 15261 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Ashlock, Melissa
论文数: 0 引用数: 0
h-index: 0
机构:
Cyst Fibrosis Fdn Therapeut Inc, Bethesda, MD 20814 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA

Negulescu, Paul
论文数: 0 引用数: 0
h-index: 0
机构:
Vertex Pharmaceut Inc, San Diego, CA 92121 USA Vertex Pharmaceut Inc, San Diego, CA 92121 USA