AAV8-mediated liver-directed gene therapy corrects blood phenylalanine in murine PKU.

被引：0
|
作者：
Harding, CO
Gillingham, MB
Hamman, K
Clark, H
Koeberl, D
机构：
[1] Oregon Hlth & Sci Univ, Portland, OR 97201 USA
[2] Duke Univ, Durham, NC USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2005年 / 84卷 / 03期
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中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
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页码：222 / 222
页数：1
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