Precious SMA natural history data A benchmark to measure future treatment successes

被引：22

作者：

Darras, Basil T. ^{[1
]}

De Vivo, Darryl C. ^{[2
]}

机构：

[1] Boston Childrens Hosp, Dept Neurol, Neuromuscular Program, Boston, MA USA

[2] Columbia Univ, Pediat Neurol Serv, Irving Med Ctr, New York, NY USA

来源：

NEUROLOGY | 2018年 / 91卷 / 08期

关键词：

MUSCULAR-ATROPHY;

D O I：

10.1212/WNL.0000000000006026

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

引用

页码：337 / 339

页数：3

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