共 8 条
[1]
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
[J].
Finkel, R. S.
;
Mercuri, E.
;
Darras, B. T.
;
Connolly, A. M.
;
Kuntz, N. L.
;
Kirschner, J.
;
Chiriboga, C. A.
;
Saito, K.
;
Servais, L.
;
Tizzano, E.
;
Topaloglu, H.
;
Tulinius, M.
;
Montes, J.
;
Glanzman, A. M.
;
Bishop, K.
;
Zhong, Z. J.
;
Gheuens, S.
;
Bennett, C. F.
;
Schneider, E.
;
Farwell, W.
;
De Vivo, D. C.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2017, 377 (18)
:1723-1732

Finkel, R. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Mercuri, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Catholic Univ, Dept Pediat Neurol, Rome, Italy Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Darras, B. T.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Dept Neurol, Boston, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Connolly, A. M.
论文数: 0 引用数: 0
h-index: 0
机构:
St Louis Childrens Hosp, Dept Neurol, St Louis, MO 63178 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Kuntz, N. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Ann & Robert H Lurie Childrens Hosp Chicago, Dept Pediat, Chicago, IL 60611 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Kirschner, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Freiburg, Fac Med, Med Ctr, Dept Neuropediat & Muscle Disorders, Freiburg, Germany Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Chiriboga, C. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Dept Neurol, New York, NY USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Saito, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Tokyo Womens Med Coll, Inst Med Genet, Tokyo, Japan
Tokyo Womens Med Coll, Dept Pediat, Tokyo, Japan Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Servais, L.
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Mot, Paris, France Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Tizzano, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Vall dHebron, Dept Clin & Mol Genet, Barcelona, Spain
Univ Hosp Vall dHebron, Rare Dis Unit, Barcelona, Spain
Ctr Invest Biomed Enfermedades Raras CIBERER, Barcelona, Spain Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Topaloglu, H.
论文数: 0 引用数: 0
h-index: 0
机构:
Hacettepe Univ, Sch Med, Dept Pediat, Ankara, Turkey Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Tulinius, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Gothenburg Univ, Queen Silvia Childrens Hosp, Dept Pediat, Gothenburg, Sweden Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Montes, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Dept Neurol, New York, NY USA
Columbia Univ, Dept Rehabil & Regenerat Med, New York, NY USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Glanzman, A. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Dept Phys Therapy, Philadelphia, PA 19104 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Bishop, K.
论文数: 0 引用数: 0
h-index: 0
机构:
lonis Pharmaceut, Carlsbad, CA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Zhong, Z. J.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Gheuens, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Bennett, C. F.
论文数: 0 引用数: 0
h-index: 0
机构:
lonis Pharmaceut, Carlsbad, CA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Schneider, E.
论文数: 0 引用数: 0
h-index: 0
机构:
lonis Pharmaceut, Carlsbad, CA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

Farwell, W.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA

De Vivo, D. C.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Dept Neurol, Med Ctr, New York, NY USA
Columbia Univ, Dept Pediat, Med Ctr, New York, NY 10027 USA Nemours Childrens Hosp, Dept Pediat, Div Neurol, 13535 Nemours Pkwy,5th Fl, Orlando, FL 32827 USA
[2]
Nusinersen in adults with 5q spinal muscular atrophy: a non-interventional, multicentre, observational cohort study
[J].
Hagenacker, Tim
;
Wurster, Claudia D.
;
Guenther, Rene
;
Schreiber-Katz, Olivia
;
Osmanovic, Alma
;
Petri, Susanne
;
Weiler, Markus
;
Ziegler, Andreas
;
Kuttler, Josua
;
Koch, Jan C.
;
Schneider, Ilka
;
Wunderlich, Gilbert
;
Schloss, Natalie
;
Lehmann, Helmar C.
;
Cordts, Isabell
;
Deschauer, Marcus
;
Lingor, Paul
;
Kamm, Christoph
;
Stolte, Benjamin
;
Pietruck, Lena
;
Totzeck, Andreas
;
Kizina, Kathrin
;
Monninghoff, Christoph
;
von Velsen, Otgonzul
;
Ose, Claudia
;
Reichmann, Heinz
;
Forsting, Michael
;
Pechmann, Astrid
;
Kirschner, Janbernd
;
Ludolph, Albert C.
;
Hermann, Andreas
;
Kleinschnitz, Christoph
.
LANCET NEUROLOGY,
2020, 19 (04)
:317-325

Hagenacker, Tim
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Wurster, Claudia D.
论文数: 0 引用数: 0
h-index: 0
机构:
Ulm Univ, Dept Neurol, Ulm, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Guenther, Rene
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Dresden, Univ Klinikum Carl Gustav Carus, Dept Neurol, Dresden, Germany
German Ctr Neurodegenerat Dis Dresden, Dresden, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Schreiber-Katz, Olivia
论文数: 0 引用数: 0
h-index: 0
机构:
Hannover Med Sch, Dept Neurol, Hannover, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Osmanovic, Alma
论文数: 0 引用数: 0
h-index: 0
机构:
Hannover Med Sch, Dept Neurol, Hannover, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Petri, Susanne
论文数: 0 引用数: 0
h-index: 0
机构:
Hannover Med Sch, Dept Neurol, Hannover, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Weiler, Markus
论文数: 0 引用数: 0
h-index: 0
机构:
Heidelberg Univ Hosp, Dept Neurol, Heidelberg, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Ziegler, Andreas
论文数: 0 引用数: 0
h-index: 0
机构:
Heidelberg Univ Hosp, Ctr Child & Adolescent Med, Div Child Neurol & Metab Med, Heidelberg, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Kuttler, Josua
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Gottingen, Dept Neurol, Gottingen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Koch, Jan C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Med Gottingen, Dept Neurol, Gottingen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Schneider, Ilka
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Halle Saale, Dept Neurol, Halle, Saale, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Wunderlich, Gilbert
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cologne, Fac Med, Dept Neurol, Cologne, Germany
Univ Cologne, Fac Med, Ctr Rare Dis, Cologne, Germany
Univ Cologne, Univ Hosp Cologne, Cologne, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Schloss, Natalie
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cologne, Fac Med, Dept Neurol, Cologne, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Lehmann, Helmar C.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cologne, Fac Med, Dept Neurol, Cologne, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Cordts, Isabell
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Dept Neurol, Klinikum Rechts Isar, Munich, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Deschauer, Marcus
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Dept Neurol, Klinikum Rechts Isar, Munich, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Lingor, Paul
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Munich, Dept Neurol, Klinikum Rechts Isar, Munich, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

论文数: 引用数:
h-index:
机构:

Stolte, Benjamin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Pietruck, Lena
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Totzeck, Andreas
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Kizina, Kathrin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Monninghoff, Christoph
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Essen, Dept Diagnost & Intervent Radiol & Neuroradiol, Essen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

von Velsen, Otgonzul
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Essen, Inst Med Informat Biometr & Epidemiol, Essen, Germany
Univ Hosp Essen, Ctr Clin Trials, Essen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Ose, Claudia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Essen, Inst Med Informat Biometr & Epidemiol, Essen, Germany
Univ Hosp Essen, Ctr Clin Trials, Essen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Reichmann, Heinz
论文数: 0 引用数: 0
h-index: 0
机构:
Tech Univ Dresden, Univ Klinikum Carl Gustav Carus, Dept Neurol, Dresden, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Forsting, Michael
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Essen, Dept Diagnost & Intervent Radiol & Neuroradiol, Essen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Pechmann, Astrid
论文数: 0 引用数: 0
h-index: 0
机构:
Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, Freiburg, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Kirschner, Janbernd
论文数: 0 引用数: 0
h-index: 0
机构:
Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, Freiburg, Germany
Univ Med Ctr Bonn, Dept Neuropediat, Bonn, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Ludolph, Albert C.
论文数: 0 引用数: 0
h-index: 0
机构:
Ulm Univ, Dept Neurol, Ulm, Germany
German Ctr Neurodegenerat Dis Ulm, Ulm, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Hermann, Andreas
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rostock, Dept Neurol, Rostock, Germany
Univ Rostock, Univ Med Ctr Rostock, Dept Neurol, Translat Neurodegenerat Sect Albrecht Kosser, Rostock, Germany
German Ctr Neurodegenerat Dis Rostock, Rostock, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany

Kleinschnitz, Christoph
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany Univ Hosp Essen, Dept Neurol, D-45127 Essen, Germany
[3]
Nusinersen: Evidence of sustained clinical improvement and lessened fatigue in older ambulatory patients with spinal muscular atrophy
[J].
McMillan, Hugh J.
.
MUSCLE & NERVE,
2020, 61 (01)
:1-2

McMillan, Hugh J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Ottawa, Childrens Hosp Eastern Ontario, Div Neurol, Ottawa, ON, Canada Univ Ottawa, Childrens Hosp Eastern Ontario, Div Neurol, Ottawa, ON, Canada
[4]
Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy
[J].
Mercuri, E.
;
Darras, B. T.
;
Chiriboga, C. A.
;
Day, J. W.
;
Campbell, C.
;
Connolly, A. M.
;
Iannaccone, S. T.
;
Kirschner, J.
;
Kuntz, N. L.
;
Saito, K.
;
Shieh, P. B.
;
Tulinius, M.
;
Mazzone, E. S.
;
Montes, J.
;
Bishop, K. M.
;
Yang, Q.
;
Foster, R.
;
Gheuens, S.
;
Bennett, C. F.
;
Farwell, W.
;
Schneider, E.
;
De Vivo, D. C.
;
Finkel, R. S.
;
Bradley, Walter G.
;
Kaufmann, Petra
;
Dickson, Patricia I.
;
Reingold, Stephen C.
;
Davis, Charles S.
;
Arredondo, Kristen
;
Castro, Diana
;
Cowie, Margaret
;
Farrow-Gillespie, Alan
;
Hebert, Andrew
;
Kauk, Melissa
;
Miller, Nancy
;
Nelson, Leslie
;
Spain, Thomas, Jr.
;
Cappell, Joshua
;
Constantinescu, Andrei
;
Cruz, Rosangel
;
Dastgir, Jahannaz
;
De Vivo, Darryl
;
Dunaway, Sally
;
Engelstad, Kristin
;
Khandji, Alexander G.
;
Kramer, Samantha
;
Marra, Jonathan
;
Popolizio, Molly
;
Salazar, Rachel
;
Weimer, Louis H.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2018, 378 (07)
:625-635

Mercuri, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Catholic Univ, Dept Pediat Neurol, Rome, Italy Catholic Univ, Dept Pediat Neurol, Rome, Italy

Darras, B. T.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Dept Neurol, Boston, MA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Chiriboga, C. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ Med Ctr, Dept Neurol, New York, NY USA
Columbia Univ Med Ctr, Dept Pediat, New York, NY USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Day, J. W.
论文数: 0 引用数: 0
h-index: 0
机构:
Stanford Sch Med, Dept Neurol, Stanford, CA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Campbell, C.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp, London Hlth Sci Ctr, London, ON, Canada Catholic Univ, Dept Pediat Neurol, Rome, Italy

Connolly, A. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Washington Univ, Sch Med, Dept Neurol, St Louis, MO 63110 USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Iannaccone, S. T.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Kirschner, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Freiburg, Med Ctr, Fac Med, Dept Neuropediat & Muscle Disorders, Freiburg, Germany Catholic Univ, Dept Pediat Neurol, Rome, Italy

Kuntz, N. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Ann & Robert H Lurie Childrens Hosp Chicago, Dept Pediat, Chicago, IL 60611 USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Saito, K.
论文数: 0 引用数: 0
h-index: 0
机构:
Tokyo Womens Med Univ, Inst Med Genet, Tokyo, Japan
Tokyo Womens Med Univ, Dept Pediat, Tokyo, Japan Catholic Univ, Dept Pediat Neurol, Rome, Italy

Shieh, P. B.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Los Angeles, David Geffen Sch Med, Los Angeles, CA 90095 USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Tulinius, M.
论文数: 0 引用数: 0
h-index: 0
机构:
Gothenburg Univ, Queen Silvia Childrens Hosp, Dept Pediat, Gothenburg, Sweden Catholic Univ, Dept Pediat Neurol, Rome, Italy

Mazzone, E. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Catholic Univ, Dept Pediat Neurol, Rome, Italy Catholic Univ, Dept Pediat Neurol, Rome, Italy

Montes, J.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ Med Ctr, Dept Neurol, New York, NY USA
Columbia Univ Med Ctr, Dept Rehabil & Regenerat Med, New York, NY USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Bishop, K. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Yang, Q.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Foster, R.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Gheuens, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Bennett, C. F.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Farwell, W.
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Cambridge, MA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Schneider, E.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut, Carlsbad, CA USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

De Vivo, D. C.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ Med Ctr, Dept Neurol, New York, NY USA
Columbia Univ Med Ctr, Dept Pediat, New York, NY USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Finkel, R. S.
论文数: 0 引用数: 0
h-index: 0
机构:
Nemours Childrens Hosp, Dept Pediat, Div Neurol, Orlando, FL USA Catholic Univ, Dept Pediat Neurol, Rome, Italy

Bradley, Walter G.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Kaufmann, Petra
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Dickson, Patricia I.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Reingold, Stephen C.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Davis, Charles S.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Arredondo, Kristen
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Castro, Diana
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Cowie, Margaret
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Farrow-Gillespie, Alan
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Hebert, Andrew
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Kauk, Melissa
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Miller, Nancy
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Nelson, Leslie
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Spain, Thomas, Jr.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Cappell, Joshua
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Constantinescu, Andrei
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h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Cruz, Rosangel
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Dastgir, Jahannaz
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

De Vivo, Darryl
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Dunaway, Sally
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Engelstad, Kristin
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Khandji, Alexander G.
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Kramer, Samantha
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Marra, Jonathan
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Popolizio, Molly
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Salazar, Rachel
论文数: 0 引用数: 0
h-index: 0
机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy

Weimer, Louis H.
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机构: Catholic Univ, Dept Pediat Neurol, Rome, Italy
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Patterns of disease progression in type 2 and 3 SMA: Implications for clinical trials
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Ramsey, Danielle
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Mayhew, Anna
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Glanzman, Allan M.
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Dunaway, Sally
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Salazar, Rachel
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Pasternak, Amy
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Quigley, Janet
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Pane, Marika
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Scoto, Mariacristina
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Messina, Sonia
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Sframeli, Maria
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Vita, Gian Luca
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D'Amico, Adele
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van den Hauwe, Marleen
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Sivo, Serena
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Goemans, Nathalie
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Mercuri, Eugenio
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Finkel, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cent Florida, Coll Med, Nemours Childrens Hosp, Orlando, FL 32816 USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Montes, Jacqueline
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Mazzone, Elena S.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Sormani, Maria Pia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Genoa, Dept Hlth Sci, Biostat Unit, Genoa, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Main, Marion
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
Great Ormond St Hosp Sick Children, London, England Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Ramsey, Danielle
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
Great Ormond St Hosp Sick Children, London, England Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Mayhew, Anna
论文数: 0 引用数: 0
h-index: 0
机构:
Newcastle Univ, Inst Med Genet, Newcastle Upon Tyne, Tyne & Wear, England Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Glanzman, Allan M.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Dept Phys Therapy, Philadelphia, PA 19104 USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Dunaway, Sally
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Salazar, Rachel
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Pasternak, Amy
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Neurol, Boston Childrens Hosp, Boston, MA 02115 USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Quigley, Janet
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Neurol, Boston Childrens Hosp, Boston, MA 02115 USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Pane, Marika
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Pera, Maria Carmela
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Scoto, Mariacristina
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
Great Ormond St Hosp Sick Children, London, England Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

论文数: 引用数:
h-index:
机构:

Sframeli, Maria
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Messina, Dept Neurosci, Messina, Italy
Univ Messina, Nemo Sud Clin Ctr, Messina, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Vita, Gian Luca
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Messina, Dept Neurosci, Messina, Italy
Univ Messina, Nemo Sud Clin Ctr, Messina, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

D'Amico, Adele
论文数: 0 引用数: 0
h-index: 0
机构:
IRCCS, Bambino Gesu Childrens Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Disorders, Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

van den Hauwe, Marleen
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Leuven, Dept Child Neurol, Leuven, Belgium Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Sivo, Serena
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Goemans, Nathalie
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Hosp Leuven, Dept Child Neurol, Leuven, Belgium Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Kaufmann, Petra
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Darras, Basil T.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Dept Neurol, Boston Childrens Hosp, Boston, MA 02115 USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Bertini, Enrico
论文数: 0 引用数: 0
h-index: 0
机构:
IRCCS, Bambino Gesu Childrens Hosp, Dept Neurosci, Unit Neuromuscular & Neurodegenerat Disorders, Rome, Italy Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

Muntoni, Francesco
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
Great Ormond St Hosp Sick Children, London, England Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy

De Vivo, Darryl C.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Med Ctr, Dept Neurol, New York, NY USA Univ Cattolica Sacro Cuore, Dept Paediat Neurol, I-00168 Rome, Italy
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Montes, Jacqueline
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Darras, Basil T.
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Muntoni, Francesco
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Montes, Jacqueline
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Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA
Columbia Univ, Dept Neurol, Irving Med Ctr, New York, NY 10032 USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Young, Sally Dunaway
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h-index: 0
机构:
Stanford Univ, Sch Med, Dept Neurol, Palo Alto, CA 94304 USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Mazzone, Elena S.
论文数: 0 引用数: 0
h-index: 0
机构:
Catholic Univ, Dept Paediat Neurol, Rome, Italy Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Pasternak, Amy
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Dept Neurol, Boston, MA USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Glanzman, Allan M.
论文数: 0 引用数: 0
h-index: 0
机构:
Childrens Hosp Philadelphia, Dept Phys Therapy, Philadelphia, PA 19104 USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Finkel, Richard S.
论文数: 0 引用数: 0
h-index: 0
机构:
Nemours Childrens Hosp, Dept Pediat, Div Neurol, Orlando, FL USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Darras, Basil T.
论文数: 0 引用数: 0
h-index: 0
机构:
Boston Childrens Hosp, Dept Neurol, Boston, MA USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Muntoni, Francesco
论文数: 0 引用数: 0
h-index: 0
机构:
UCL Great Ormond St Inst Child Hlth, Dubowitz Neuromuscular Ctr, London, England
NIHR Great Ormond St Hosp Biomed Res Ctr, London, England Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Mercuri, Eugenio
论文数: 0 引用数: 0
h-index: 0
机构:
Catholic Univ, Dept Paediat Neurol, Rome, Italy Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

De Vivo, Darryl C.
论文数: 0 引用数: 0
h-index: 0
机构:
Columbia Univ, Dept Neurol, Irving Med Ctr, New York, NY 10032 USA
Columbia Univ, Dept Pediat, Irving Med Ctr, New York, NY 10032 USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Bishop, Kathie M.
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut Inc, Clin Dev & Antisense Res, Carlsbad, CA USA
Otonomy Inc, 4796 Execut Dr, San Diego, CA 92121 USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Schneider, Eugene
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut Inc, Clin Dev & Antisense Res, Carlsbad, CA USA
Otonomy Inc, 4796 Execut Dr, San Diego, CA 92121 USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Bennett, C. Frank
论文数: 0 引用数: 0
h-index: 0
机构:
Ionis Pharmaceut Inc, Clin Dev & Antisense Res, Carlsbad, CA USA
Otonomy Inc, 4796 Execut Dr, San Diego, CA 92121 USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Foster, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Biostat, Maidenhead, Berks, England Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA

Farwell, Wildon
论文数: 0 引用数: 0
h-index: 0
机构:
Biogen, Clin Dev, Cambridge, MA USA Columbia Univ, Irving Med Ctr, Dept Rehabil & Regenerat Med, New York, NY 10032 USA
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Veerapandiyan, Aravindhan
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Kwon, Jennifer
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Collins, Erin
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Ciafaloni, Emma
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MUSCLE & NERVE,
2020, 61 (02)
:222-226

Veerapandiyan, Aravindhan
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Arkansas Med Sci, Arkansas Childrens Hosp, Div Neurol, Dept Pediat, Little Rock, AR 72205 USA Univ Arkansas Med Sci, Arkansas Childrens Hosp, Div Neurol, Dept Pediat, Little Rock, AR 72205 USA

Eichinger, Katy
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Med Ctr, Dept Neurol, Div Neuromuscular Med, Rochester, NY 14642 USA Univ Arkansas Med Sci, Arkansas Childrens Hosp, Div Neurol, Dept Pediat, Little Rock, AR 72205 USA

Guntrum, Debra
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Med Ctr, Dept Neurol, Div Neuromuscular Med, Rochester, NY 14642 USA Univ Arkansas Med Sci, Arkansas Childrens Hosp, Div Neurol, Dept Pediat, Little Rock, AR 72205 USA

Kwon, Jennifer
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Wisconsin, Dept Neurol, Sch Med & Publ Hlth, Div Pediat Neurol, Madison, WI 53706 USA Univ Arkansas Med Sci, Arkansas Childrens Hosp, Div Neurol, Dept Pediat, Little Rock, AR 72205 USA

Baker, Lindsay
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Med Ctr, Dept Neurol, Div Neuromuscular Med, Rochester, NY 14642 USA Univ Arkansas Med Sci, Arkansas Childrens Hosp, Div Neurol, Dept Pediat, Little Rock, AR 72205 USA

Collins, Erin
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Med Ctr, Dept Neurol, Div Neuromuscular Med, Rochester, NY 14642 USA Univ Arkansas Med Sci, Arkansas Childrens Hosp, Div Neurol, Dept Pediat, Little Rock, AR 72205 USA

Ciafaloni, Emma
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Med Ctr, Dept Neurol, Div Neuromuscular Med, Rochester, NY 14642 USA Univ Arkansas Med Sci, Arkansas Childrens Hosp, Div Neurol, Dept Pediat, Little Rock, AR 72205 USA
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Safety and Treatment Effects of Nusinersen in Longstanding Adult 5q-SMA Type 3-A Prospective Observational Study
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Walter, Maggie C.
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Wenninger, Stephan
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Thiele, Simone
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Stauber, Julia
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Hiebeler, Miriam
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Greckl, Eva
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Stahl, Kristina
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Pechmann, Astrid
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Lochmueller, Hanns
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Kirschner, Janbernd
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Schoser, Benedikt
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JOURNAL OF NEUROMUSCULAR DISEASES,
2019, 6 (04)
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Walter, Maggie C.
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h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

Wenninger, Stephan
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

Thiele, Simone
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

Stauber, Julia
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

Hiebeler, Miriam
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

Greckl, Eva
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

Stahl, Kristina
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

Pechmann, Astrid
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, Freiburg, Germany Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

Lochmueller, Hanns
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Freiburg, Dept Neuropediat & Muscle Disorders, Med Ctr, Fac Med, Freiburg, Germany
Childrens Hosp Eastern Ontario, Res Inst, Ottawa, ON, Canada
Ottawa Hosp, Dept Med, Div Neurol, Ottawa, ON, Canada Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

Kirschner, Janbernd
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Freiburg, Med Ctr Univ Freiburg, Fac Med, Dept Neuropediat & Muscle Disorders, Freiburg, Germany
Rheinische Friedrich Wilhelms Univ Bonn, Dept Neuropaediat, Bonn, Germany Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

Schoser, Benedikt
论文数: 0 引用数: 0
h-index: 0
机构:
Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany