Safety of Adeno-associated virus-based vector-mediated gene therapy-impact of vector dose

被引：38

作者：

Maurya, Shubham ^{[1
,2
]}

Sarangi, Pratiksha ^{[1
,2
]}

Jayandharan, Giridhara R. ^{[1
,2
]}

机构：

[1] Indian Inst Technol Kanpur, Dept Biol Sci & Bioengn, Kanpur, Uttar Pradesh, India

[2] Indian Inst Technol Kanpur, Mehta Family Ctr Engn Med, Kanpur, Uttar Pradesh, India

来源：

CANCER GENE THERAPY | 2022年 / 29卷 / 10期

关键词：

D O I：

10.1038/s41417-021-00413-6

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：1305 / 1306

页数：2

共 50 条

[41] Cardiac gene therapy with adeno-associated virus-based vectors [J].

Chamberlain, Kyle ;

Riyad, Jalish M. ;

Weber, Thomas .

CURRENT OPINION IN CARDIOLOGY, 2017, 32 (03) :275-282

[42] Adeno-Associated Virus-Based Gene Therapy for CNS Diseases [J].

Hocquemiller, Michael ;

Giersch, Laura ;

Audrain, Mickael ;

Parker, Samantha ;

Cartier, Nathalie .

HUMAN GENE THERAPY, 2016, 27 (07) :478-496

[43] Adeno-associated virus-based gene therapy for inherited disorders [J].

Flotte, TR .

PEDIATRIC RESEARCH, 2005, 58 (06) :1143-1147

[44] Adeno-associated virus-based vectors and their application for gene therapy [J].

Serra, C ;

Zentilin, L ;

Giacca, M .

MINERVA BIOTECNOLOGICA, 1996, 8 (03) :183-190

[45] Adeno-associated virus as a gene therapy vector: Vector development, production and clinical applications [J].

Grieger, JC ;

Samulski, RJ .

GENE THERAPY AND GENE DELIVERY SYSTEMS, 2005, 99 :119-145

[46] Characterization of Adeno-Associated Viral Vector-Mediated Human Factor VIII Gene Therapy in Hemophilia A Mice [J].

Greig, Jenny A. ;

Wang, Qiang ;

Reicherter, Amanda L. ;

Chen, Shu-Jen ;

Hanlon, Alexandra L. ;

Tipper, Christopher H. ;

Clark, K. Reed ;

Wadsworth, Samuel ;

Wang, Lili ;

Wilson, James M. .

HUMAN GENE THERAPY, 2017, 28 (05) :392-402

[47] Silencing of T lymphocytes by antigen-driven programmed death in recombinant adeno-associated virus vector-mediated gene therapy [J].

Velazquez, Victoria M. ;

Bowen, David G. ;

Walker, Christopher M. .

BLOOD, 2009, 113 (03) :538-545

[48] Efficacious Androgen Hormone Administration in Combination with Adeno-Associated Virus Vector-Mediated Gene Therapy in Female Mice with Pompe Disease [J].

Han, Sang-oh ;

Gheorghiu, Dorothy ;

Chang, Alex ;

Mapatano, Sweet Hope ;

Li, Songtao ;

Brooks, Elizabeth ;

Koeberl, Dwight .

HUMAN GENE THERAPY, 2022, 33 (9-10) :479-491

[49] Erratum: Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia [J].

D D Koeberl ;

B D Sun ;

T V Damodaran ;

T Brown ;

D S Millington ;

D K Benjamin ;

A Bird ;

A Schneider ;

S Hillman ;

M Jackson ;

R M Beaty ;

Y T Chen .

Gene Therapy, 2007, 14 :281-281

[50] Erratum: Early, sustained efficacy of adeno-associated virus vector-mediated gene therapy in glycogen storage disease type Ia [J].