共 49 条
[1]
Long-Term Effect of Gene Therapy on Leber's Congenital Amaurosis
[J].
Bainbridge, J. W. B.
;
Mehat, M. S.
;
Sundaram, V.
;
Robbie, S. J.
;
Barker, S. E.
;
Ripamonti, C.
;
Georgiadis, A.
;
Mowat, F. M.
;
Beattie, S. G.
;
Gardner, P. J.
;
Feathers, K. L.
;
Luong, V. A.
;
Yzer, S.
;
Balaggan, K.
;
Viswanathan, A.
;
de Ravel, T. J. L.
;
Casteels, I.
;
Holder, G. E.
;
Tyler, N.
;
Fitzke, F. W.
;
Weleber, R. G.
;
Nardini, M.
;
Moore, A. T.
;
Thompson, D. A.
;
Petersen-Jones, S. M.
;
Michaelides, M.
;
van den Born, L. I.
;
Stockman, A.
;
Smith, A. J.
;
Rubin, G.
;
Ali, R. R.
.
NEW ENGLAND JOURNAL OF MEDICINE,
2015, 372 (20)
:1887-1897

Bainbridge, J. W. B.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Mehat, M. S.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Sundaram, V.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Robbie, S. J.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Barker, S. E.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Ripamonti, C.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Georgiadis, A.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Mowat, F. M.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Michigan State Univ, Coll Vet Med, E Lansing, MI 48824 USA UCL, Inst Ophthalmol, London EC1V 9EL, England

Beattie, S. G.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Gardner, P. J.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Feathers, K. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Michigan, Kellogg Eye Ctr, Sch Med, Ann Arbor, MI 48109 USA UCL, Inst Ophthalmol, London EC1V 9EL, England

Luong, V. A.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Yzer, S.
论文数: 0 引用数: 0
h-index: 0
机构:
Rotterdam Eye Hosp, Rotterdam, Netherlands UCL, Inst Ophthalmol, London EC1V 9EL, England

Balaggan, K.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Viswanathan, A.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

de Ravel, T. J. L.
论文数: 0 引用数: 0
h-index: 0
机构:
Katholieke Univ Leuven, Ctr Human Genet, Leuven, Belgium UCL, Inst Ophthalmol, London EC1V 9EL, England

Casteels, I.
论文数: 0 引用数: 0
h-index: 0
机构:
UZ Leuven, Dept Ophthalmol, Leuven, Belgium UCL, Inst Ophthalmol, London EC1V 9EL, England

Holder, G. E.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Tyler, N.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Dept Civil Environm & Geomat Engn, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Fitzke, F. W.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Weleber, R. G.
论文数: 0 引用数: 0
h-index: 0
机构:
Oregon Hlth & Sci Univ, Casey Eye Inst, Oregon Retinal Degenerat Ctr, Ophthalm Genet Serv, Portland, OR 97201 USA UCL, Inst Ophthalmol, London EC1V 9EL, England

Nardini, M.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Univ Durham, Dept Psychol, Durham DH1 3LE, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Moore, A. T.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Thompson, D. A.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Michigan, Kellogg Eye Ctr, Sch Med, Ann Arbor, MI 48109 USA UCL, Inst Ophthalmol, London EC1V 9EL, England

Petersen-Jones, S. M.
论文数: 0 引用数: 0
h-index: 0
机构:
Michigan State Univ, Coll Vet Med, E Lansing, MI 48824 USA UCL, Inst Ophthalmol, London EC1V 9EL, England

Michaelides, M.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Moorfields Eye Hosp, London, England UCL, Inst Ophthalmol, London EC1V 9EL, England

van den Born, L. I.
论文数: 0 引用数: 0
h-index: 0
机构:
Rotterdam Eye Hosp, Rotterdam, Netherlands UCL, Inst Ophthalmol, London EC1V 9EL, England

Stockman, A.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Smith, A. J.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Rubin, G.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England UCL, Inst Ophthalmol, London EC1V 9EL, England

Ali, R. R.
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, Inst Ophthalmol, London EC1V 9EL, England
Univ Michigan, Kellogg Eye Ctr, Sch Med, Ann Arbor, MI 48109 USA UCL, Inst Ophthalmol, London EC1V 9EL, England
[2]
Histopathologic and immunocytochemical analysis of the retina and ocular tissues in Batten disease
[J].
Bensaoula, T
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Shibuya, H
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Katz, ML
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Smith, JE
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Johnson, GS
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John, SK
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Milam, AH
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OPHTHALMOLOGY,
2000, 107 (09)
:1746-1753

Bensaoula, T
论文数: 0 引用数: 0
h-index: 0
机构: Univ Penn, Scheie Eye Inst, Philadelphia, PA 19104 USA

Shibuya, H
论文数: 0 引用数: 0
h-index: 0
机构: Univ Penn, Scheie Eye Inst, Philadelphia, PA 19104 USA

Katz, ML
论文数: 0 引用数: 0
h-index: 0
机构: Univ Penn, Scheie Eye Inst, Philadelphia, PA 19104 USA

Smith, JE
论文数: 0 引用数: 0
h-index: 0
机构: Univ Penn, Scheie Eye Inst, Philadelphia, PA 19104 USA

Johnson, GS
论文数: 0 引用数: 0
h-index: 0
机构: Univ Penn, Scheie Eye Inst, Philadelphia, PA 19104 USA

John, SK
论文数: 0 引用数: 0
h-index: 0
机构: Univ Penn, Scheie Eye Inst, Philadelphia, PA 19104 USA

Milam, AH
论文数: 0 引用数: 0
h-index: 0
机构: Univ Penn, Scheie Eye Inst, Philadelphia, PA 19104 USA
[3]
Gene therapy for lysosomal storage disorders: a good start
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Biffi, Alessandra
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HUMAN MOLECULAR GENETICS,
2016, 25
:R65-R75

Biffi, Alessandra
论文数: 0 引用数: 0
h-index: 0
机构:
Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy
Boston Childrens Hosp, Gene Therapy Program, Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA 02115 USA
Boston Childrens Hosp, Dept Med, Program Gene Therapy Rare Dis, Boston, MA 02115 USA Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy
[4]
Use of model organisms for the study of neuronal ceroid lipofuscinosis
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Bond, Michael
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Holthaus, Sophia-Martha Kleine
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Tammen, Imke
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Tear, Guy
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Russell, Claire
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BIOCHIMICA ET BIOPHYSICA ACTA-MOLECULAR BASIS OF DISEASE,
2013, 1832 (11)
:1842-1865

Bond, Michael
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, MRC Lab Mol Cell Biol, London WC1E 6BT, England UCL, MRC Lab Mol Cell Biol, London WC1E 6BT, England

Holthaus, Sophia-Martha Kleine
论文数: 0 引用数: 0
h-index: 0
机构:
UCL, MRC Lab Mol Cell Biol, London WC1E 6BT, England
UCL Inst Ophthalmol, Dept Genet, London EC1V 9EL, England UCL, MRC Lab Mol Cell Biol, London WC1E 6BT, England

Tammen, Imke
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Sydney, Fac Vet Sci, ReproGen, Camden, NSW 2570, Australia UCL, MRC Lab Mol Cell Biol, London WC1E 6BT, England

Tear, Guy
论文数: 0 引用数: 0
h-index: 0
机构:
Kings Coll London, MRC Ctr Dev Neurobiol, London SE1 1UL, England UCL, MRC Lab Mol Cell Biol, London WC1E 6BT, England

Russell, Claire
论文数: 0 引用数: 0
h-index: 0
机构:
Univ London Royal Vet Coll, Dept Comparat Biomed Sci, London NW1 0TU, England UCL, MRC Lab Mol Cell Biol, London WC1E 6BT, England
[5]
RETINAL DEGENERATION IN THE RD MOUSE IS CAUSED BY A DEFECT IN THE BETA-SUBUNIT OF ROD CGMP-PHOSPHODIESTERASE
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BOWES, C
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LI, TS
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DANCIGER, M
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BAXTER, LC
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APPLEBURY, ML
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FARBER, DB
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NATURE,
1990, 347 (6294)
:677-680

BOWES, C
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,JULES STEIN EYE INST,LOS ANGELES,CA 90024

LI, TS
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,JULES STEIN EYE INST,LOS ANGELES,CA 90024

DANCIGER, M
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,JULES STEIN EYE INST,LOS ANGELES,CA 90024

BAXTER, LC
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,JULES STEIN EYE INST,LOS ANGELES,CA 90024

APPLEBURY, ML
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,JULES STEIN EYE INST,LOS ANGELES,CA 90024

FARBER, DB
论文数: 0 引用数: 0
h-index: 0
机构: UNIV CALIF LOS ANGELES,SCH MED,JULES STEIN EYE INST,LOS ANGELES,CA 90024
[6]
Clinical and molecular characterization of non-syndromic retinal dystrophy due to c.175G>A mutation in ceroid lipofuscinosis neuronal 3 (CLN3)
[J].
Chen, Fred K.
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Zhang, Xiao
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Eintracht, Jonathan
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Zhang, Dan
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Arunachalam, Sukanya
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Thompson, Jennifer A.
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Chelva, Enid
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Mallon, Dominic
;
Chen, Shang-Chih
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McLaren, Terri
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Lamey, Tina
;
De Roach, John
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McLenachan, Samuel
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DOCUMENTA OPHTHALMOLOGICA,
2019, 138 (01)
:55-70

Chen, Fred K.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia
Lions Eye Inst, Ocular Tissue Engn Lab, 2 Verdun St, Nedlands, WA, Australia
Royal Perth Hosp, Dept Ophthalmol, Perth, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

Zhang, Xiao
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia
Lions Eye Inst, Ocular Tissue Engn Lab, 2 Verdun St, Nedlands, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

Eintracht, Jonathan
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia
Lions Eye Inst, Ocular Tissue Engn Lab, 2 Verdun St, Nedlands, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

Zhang, Dan
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia
Lions Eye Inst, Ocular Tissue Engn Lab, 2 Verdun St, Nedlands, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

Arunachalam, Sukanya
论文数: 0 引用数: 0
h-index: 0
机构:
Lions Eye Inst, Ocular Tissue Engn Lab, 2 Verdun St, Nedlands, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

Thompson, Jennifer A.
论文数: 0 引用数: 0
h-index: 0
机构:
Sir Charles Gairdner Hosp, Australian Inherited Retinal Dis Registry, Perth, WA, Australia
Sir Charles Gairdner Hosp, Dept Med Technol & Phys, DNA Bank, Perth, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

Chelva, Enid
论文数: 0 引用数: 0
h-index: 0
机构:
Sir Charles Gairdner Hosp, Australian Inherited Retinal Dis Registry, Perth, WA, Australia
Sir Charles Gairdner Hosp, Dept Med Technol & Phys, DNA Bank, Perth, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

Mallon, Dominic
论文数: 0 引用数: 0
h-index: 0
机构:
Fiona Stanley Hosp, Dept Immunol, Perth, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

Chen, Shang-Chih
论文数: 0 引用数: 0
h-index: 0
机构:
Lions Eye Inst, Ocular Tissue Engn Lab, 2 Verdun St, Nedlands, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

McLaren, Terri
论文数: 0 引用数: 0
h-index: 0
机构:
Sir Charles Gairdner Hosp, Australian Inherited Retinal Dis Registry, Perth, WA, Australia
Sir Charles Gairdner Hosp, Dept Med Technol & Phys, DNA Bank, Perth, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

Lamey, Tina
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia
Sir Charles Gairdner Hosp, Australian Inherited Retinal Dis Registry, Perth, WA, Australia
Sir Charles Gairdner Hosp, Dept Med Technol & Phys, DNA Bank, Perth, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

De Roach, John
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia
Sir Charles Gairdner Hosp, Australian Inherited Retinal Dis Registry, Perth, WA, Australia
Sir Charles Gairdner Hosp, Dept Med Technol & Phys, DNA Bank, Perth, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia

McLenachan, Samuel
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia
Lions Eye Inst, Ocular Tissue Engn Lab, 2 Verdun St, Nedlands, WA, Australia Univ Western Australia, Ctr Ophthalmol & Visual Sci, Perth, WA, Australia
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Batten disease: features to facilitate early diagnosis
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Collins, J.
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Holder, G. E.
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Herbert, H.
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Adams, G. G. W.
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BRITISH JOURNAL OF OPHTHALMOLOGY,
2006, 90 (09)
:1119-1124

Collins, J.
论文数: 0 引用数: 0
h-index: 0
机构: Moorfields Eye Hosp, Strabismus & Paediat Serv, London EC1V 2PD, England

Holder, G. E.
论文数: 0 引用数: 0
h-index: 0
机构: Moorfields Eye Hosp, Strabismus & Paediat Serv, London EC1V 2PD, England

Herbert, H.
论文数: 0 引用数: 0
h-index: 0
机构: Moorfields Eye Hosp, Strabismus & Paediat Serv, London EC1V 2PD, England

Adams, G. G. W.
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h-index: 0
机构: Moorfields Eye Hosp, Strabismus & Paediat Serv, London EC1V 2PD, England
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Cln3Δex7/8 knock-in mice with the common JNCL mutation exhibit progressive neurologic disease that begins before birth
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Cotman, SL
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Vrbanac, V
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Lee, RL
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Johnson, KA
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HUMAN MOLECULAR GENETICS,
2002, 11 (22)
:2709-2721

Cotman, SL
论文数: 0 引用数: 0
h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA

Vrbanac, V
论文数: 0 引用数: 0
h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA

Lebel, LA
论文数: 0 引用数: 0
h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA

Lee, RL
论文数: 0 引用数: 0
h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA

Johnson, KA
论文数: 0 引用数: 0
h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA

Donahue, LR
论文数: 0 引用数: 0
h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA

Teed, AM
论文数: 0 引用数: 0
h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA

Antonellis, K
论文数: 0 引用数: 0
h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA

Bronson, RT
论文数: 0 引用数: 0
h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA

Lerner, TJ
论文数: 0 引用数: 0
h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA

MacDonald, ME
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h-index: 0
机构: Massachusetts Gen Hosp, Mol Neurogenet Unit, Charlestown, MA 02129 USA
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Efficient transduction and optogenetic stimulation of retinal bipolar cells by a synthetic adeno-associated virus capsid and promoter
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Cronin, Therese
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Vandenberghe, Luk H.
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Hantz, Peter
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Juttner, Josephine
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Reimann, Andreas
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Kacso, Agota-Eniko
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Huckfeldt, Rachel M.
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Busskamp, Volker
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Kohler, Hubertus
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Lagali, Pamela S.
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Roska, Botond
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Bennett, Jean
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EMBO MOLECULAR MEDICINE,
2014, 6 (09)
:1175-1190

论文数: 引用数:
h-index:
机构:

Vandenberghe, Luk H.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA
Harvard Univ, Massachusetts Eye & Ear Infirm, Sch Med, Schepens Eye Res Inst, Boston, MA USA Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA

论文数: 引用数:
h-index:
机构:

Juttner, Josephine
论文数: 0 引用数: 0
h-index: 0
机构:
Friedrich Miescher Inst Biomed Res, Basel, Switzerland Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA

Reimann, Andreas
论文数: 0 引用数: 0
h-index: 0
机构:
Friedrich Miescher Inst Biomed Res, Basel, Switzerland Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA

Kacso, Agota-Eniko
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Babes Bolyai, Fac Phys, R-3400 Cluj Napoca, Romania Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA

Huckfeldt, Rachel M.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA

Busskamp, Volker
论文数: 0 引用数: 0
h-index: 0
机构:
Friedrich Miescher Inst Biomed Res, Basel, Switzerland
Harvard Univ, Sch Med, Dept Genet, Boston, MA USA Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA

Kohler, Hubertus
论文数: 0 引用数: 0
h-index: 0
机构:
Friedrich Miescher Inst Biomed Res, Basel, Switzerland Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA

Lagali, Pamela S.
论文数: 0 引用数: 0
h-index: 0
机构:
Friedrich Miescher Inst Biomed Res, Basel, Switzerland
Ottawa Hosp Res Inst, Regenerat Med Program, Ottawa, ON, Canada Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA

Roska, Botond
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Friedrich Miescher Inst Biomed Res, Basel, Switzerland Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA

Bennett, Jean
论文数: 0 引用数: 0
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机构:
Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA Univ Penn, Scheie Eye Inst, Ctr Adv Retinal & Ophthalm Therapeut, FM Kirby Ctr Mol Ophthalmol, Philadelphia, PA 19104 USA
[10]
In Vivo-Directed Evolution of a New Adeno-Associated Virus for Therapeutic Outer Retinal Gene Delivery from the Vitreous
[J].
Dalkara, Deniz
;
Byrne, Leah C.
;
Klimczak, Ryan R.
;
Visel, Meike
;
Yin, Lu
;
Merigan, William H.
;
Flannery, John G.
;
Schaffer, David V.
.
SCIENCE TRANSLATIONAL MEDICINE,
2013, 5 (189)

Dalkara, Deniz
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机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Byrne, Leah C.
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h-index: 0
机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Klimczak, Ryan R.
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h-index: 0
机构:
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Visel, Meike
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机构:
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Yin, Lu
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Rochester, Flaum Eye Inst, Rochester, NY 14642 USA
Univ Rochester, Ctr Visual Sci, Rochester, NY 14642 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Merigan, William H.
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机构:
Univ Rochester, Flaum Eye Inst, Rochester, NY 14642 USA
Univ Rochester, Ctr Visual Sci, Rochester, NY 14642 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Flannery, John G.
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Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA

Schaffer, David V.
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Mol & Cellular Biol, Berkeley, CA 94720 USA
Univ Calif Berkeley, Dept Chem & Biomol Engn, Berkeley, CA 94720 USA Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA