Efforts to enhance AAV8-mediated gene therapy of Pompe disease

被引：0
|
作者：
Zieler, R. [1 ]
Bercury, S. [1 ]
Zhu, Y. [1 ]
Foley, J. [1 ]
Glimlaw, N. [1 ]
Koeberl, D. [2 ]
Scheule, R. [1 ]
Cheng, S. [1 ]
机构：
[1] Genzyme Corp, Framingham, MA 01701 USA
[2] Duke Univ, Med Ctr, Dept Pediat, Div Med Genet, Durham, NC USA
来源：
NEUROMUSCULAR DISORDERS | 2007年 / 17卷 / 9-10期
关键词：
D O I：
10.1016/j.nmd.2007.06.427
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：890 / 890
页数：1
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