Antisense oligonucleotide mediated increase in OPA1 improves mitochondrial function in fibroblasts derived from patients with autosomal dominant optic atrophy (ADOA)

被引：0
|
作者：
Venkatesh, Aditya [1 ]
Ali, Syed [1 ]
Oh, Raymond S. [1 ]
Sonntag, Donna [1 ]
Li, Zhiyu [2 ]
McKenty, Taylor [1 ]
Slim, Brittany A. [1 ]
Hufnagel, Robert B. [2 ]
Hoger, Jeffrey [1 ]
Liau, Gene [1 ]
机构：
[1] Stoke Therapeut Inc, Bedford, MA USA
[2] NIH, Bldg 10, Bethesda, MD 20892 USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2021年 / 62卷 / 08期
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中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
1482
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页数：3
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