Objective and Subjective impact of Nusinersen in Spinal Muscular Atrophy

被引:0
|
作者
Rodriguez Alvarez-Cienfuegos, J. [1 ]
Monton Alvarez, F. I. [1 ]
Gutierrez Martinez, A. [2 ]
Fregel Rodriguez, C. [1 ]
Diez, J. Aleman [1 ]
Claverie, I. Hernandez-Rojo [3 ]
机构
[1] Hosp Univ Nuestra Senora de la Candelaria, Neurol, Santa Cruz De Tenerife, Spain
[2] Complejo Hosp Univ Insular Maternoinfantil, Neurol, Las Palmas Gran Canaria, Spain
[3] Hosp Univ Severo Ochoa, Udm Afyc Madrid Sur, Madrid, Spain
关键词
D O I
暂无
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
EPO2174
引用
收藏
页码:872 / 872
页数:1
相关论文
共 50 条
  • [1] Nusinersen for spinal muscular atrophy
    Wurster, Claudia D.
    Ludolph, Albert C.
    THERAPEUTIC ADVANCES IN NEUROLOGICAL DISORDERS, 2018, 11
  • [2] Nusinersen: A Treatment for Spinal Muscular Atrophy
    Claborn, Melanie K.
    Stevens, Debra L.
    Walker, Cheri K.
    Gildon, Brooke L.
    ANNALS OF PHARMACOTHERAPY, 2019, 53 (01) : 61 - 69
  • [3] NUSINERSEN IN THE TREATMENT OF SPINAL MUSCULAR ATROPHY
    Sinko Gabriella
    Kiss Zsuzsanna
    Kalman Bernadette
    IDEGGYOGYASZATI SZEMLE-CLINICAL NEUROSCIENCE, 2018, 71 (3-4): : 90 - 94
  • [4] Nusinersen (Spinraza) for Spinal Muscular Atrophy
    不详
    MEDICAL LETTER ON DRUGS AND THERAPEUTICS, 2017, 59 (1517): : 50 - 52
  • [5] Nusinersen for adults with spinal muscular atrophy
    Arslan, Doruk
    Inan, Berin
    Kilinc, Muhammed
    Bekircan-Kurt, Can Ebru
    Erdem-Ozdamar, Sevim
    Tan, Ersin
    NEUROLOGICAL SCIENCES, 2023, 44 (07) : 2393 - 2400
  • [6] Nusinersen for adults with spinal muscular atrophy
    Doruk Arslan
    Berin Inan
    Muhammed Kilinc
    Can Ebru Bekircan-Kurt
    Sevim Erdem-Ozdamar
    Ersin Tan
    Neurological Sciences, 2023, 44 : 2393 - 2400
  • [7] Budget Impact Analysis of Nusinersen for Spinal Muscular Atrophy in China
    Duan, Chengaxin
    Ai, Dandan
    Xu, Qian
    Sui, Binyan
    Zhao, Kun
    VALUE IN HEALTH REGIONAL ISSUES, 2023, 34 : 9 - 13
  • [8] Nusinersen for the treatment of spinal muscular atrophy
    Chiriboga, Claudia A.
    EXPERT REVIEW OF NEUROTHERAPEUTICS, 2017, 17 (10) : 955 - 962
  • [9] Impact of Spinal Surgery on Intrathecal Nusinersen Injections in Pediatric Spinal Muscular Atrophy
    Aksoy, Taha
    Ramazanov, Rafik
    Yildiz, Sibel Oz
    Demirkiran, Gokhan
    Haliloglu, Goknur
    Yazici, Muharrem
    JOURNAL OF PEDIATRIC ORTHOPAEDICS, 2024, 44 (07) : e641 - e646
  • [10] Impact Of Nusinersen Treatment On Measures Of Exercise Intolerance In Spinal Muscular Atrophy
    Uher, David
    Goodwin, Ashley M.
    De Vivo, Darryl C.
    Montes, Jacqueline
    Garber, Carol Ewing
    MEDICINE & SCIENCE IN SPORTS & EXERCISE, 2023, 55 (09) : 964 - 964