Phase I/II gene therapy study for X-CGD: Results, lessons and perspectives

被引:0
作者
Grez, Manuel [1 ]
Ott, Marion G. [2 ]
Stein, Stefan [1 ]
Schultze-Strasser, Stephan [1 ]
Preiss, Carolin [1 ]
Kramer, Rolf [1 ]
Schmidt, Manfred [3 ]
Kunkel, Hana [1 ]
von Kalle, Christof [3 ]
Thrasher, Adrian [4 ]
Hoelzer, Dieter [2 ]
Seger, Reinhard [5 ]
机构
[1] Inst Biomed Res, Frankfurt, Germany
[2] Univ Med Sch, Dept Hematol Oncol, Frankfurt, Germany
[3] Natl Ctr Tumor Dis, Heidelberg, Germany
[4] Inst Child Hlth, London, England
[5] Univ Zurich, Childrens Hosp, Div Hematol Immunol, Zurich, Switzerland
关键词
D O I
10.1016/j.bcmd.2007.10.045
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
35
引用
收藏
页码:268 / 269
页数:2
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