Longitudinal changes in mNIS+7 are associated with changes in ambulatory status in hereditary transthyretin-mediated amyloidosis

被引:0
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作者
Coelho, Teresa [1 ]
Suhr, Ole [2 ]
Quan, Dianna [3 ]
Brannagan, Thomas [4 ]
Gollob, Jared [5 ]
Goyal, Sunita [5 ]
Altincatal, Arman [6 ]
Agarwal, Sonalee [5 ]
Lin, Hollis [5 ]
Adams, David [7 ]
机构
[1] Hosp Santo Antonio, Porto, Portugal
[2] Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden
[3] Univ Colorado, Aurora, CO USA
[4] Columbia Univ, New York, NY USA
[5] Alnylam Pharmaceut, Cambridge, MA USA
[6] Evidera Inc, Waltham, MA USA
[7] CHU Bicetre, AP HP, Natl Reference Ctr FAP NNERF, INSERM,U1195, Le Kremlin Bicetre, France
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R74 [神经病学与精神病学];
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页码:354 / 355
页数:2
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