[1] Univ Florida, Dept Pediat, COM, Gainesville, FL USA
[2] Univ Florida, Dept Neurosci, COM, Gainesville, FL 32610 USA
[3] Univ Alabama Birmingham, Dept Ophthalmol & Visual Sci, Birmingham, AL USA
[4] Pfizer Inc, Rare Dis Res Unit, Cambridge, MA USA
[5] Lacerta Therapeut Inc, Alachua, FL USA