Sense in Antisense Therapy for Spinal Muscular Atrophy

被引：9
作者：
MacKenzie, Alex [1 ,2 ]
机构：
[1] Childrens Hosp Eastern Ontario, Ottawa, ON K1H 8L1, Canada
[2] Univ Ottawa, Ottawa, ON, Canada
来源：
NEW ENGLAND JOURNAL OF MEDICINE | 2012年 / 366卷 / 08期
关键词：
MOUSE MODEL; RESCUE; SMN;
D O I：
10.1056/NEJMcibr1114629
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
[No abstract available]
引用
收藏
页码：761 / 763
页数：3
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