ANTISENSE-BASED EXON SKIPPING AS A THERAPY FOR DUCHENNE MUSCULAR DYSTROPHY, STATUS AND PROSPECTS

被引：0
|
作者：
van Ommen, G. -J. [1 ]
Aartsma-Rus, A. [1 ]
Evers, M. [1 ]
van Roon, W. [1 ]
'tHoen, P. -B. [1 ]
Kemaladewi, D. [1 ]
Verbeek, S. [1 ]
Yllmaz-Elis, S. [1 ]
Dauwerse, H. [2 ]
Lesnik-Oberstein, S. [2 ]
den Dunnen, J. T. [1 ]
Goemans, N. [3 ]
Tulinus, M. [4 ]
Verschuuren, J. [5 ]
de Kimpe, S. [6 ]
Campion, G. [6 ]
van Deutekom, J. [6 ]
机构：
[1] Leiden Univ, Dept Human Genet, Med Ctr, NL-2300 RA Leiden, Netherlands
[2] Leiden Univ, Dept Clin Genet, Med Ctr, Leiden, Netherlands
[3] Univ Hosp Leuven, Dept Pediat Neurol, Louvain, Belgium
[4] Univ Gothenburg, Dept Pediat, Gothenburg, Sweden
[5] Leiden Univ, Dept Neurol, Med Ctr, Leiden, Netherlands
[6] Prosensa Therapeut, Leiden, Netherlands
来源：
EUROPEAN JOURNAL OF NEUROLOGY | 2011年 / 18卷
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中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
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页码：7 / 7
页数：1
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