ANTISENSE-BASED EXON SKIPPING AS A THERAPY FOR DUCHENNE MUSCULAR DYSTROPHY, STATUS AND PROSPECTS

被引：0

作者：

van Ommen, G. -J. ^{[1
]}

Aartsma-Rus, A. ^{[1
]}

Evers, M. ^{[1
]}

van Roon, W. ^{[1
]}

'tHoen, P. -B. ^{[1
]}

Kemaladewi, D. ^{[1
]}

Verbeek, S. ^{[1
]}

Yllmaz-Elis, S. ^{[1
]}

Dauwerse, H. ^{[2
]}

Lesnik-Oberstein, S. ^{[2
]}

den Dunnen, J. T. ^{[1
]}

Goemans, N. ^{[3
]}

Tulinus, M. ^{[4
]}

Verschuuren, J. ^{[5
]}

de Kimpe, S. ^{[6
]}

Campion, G. ^{[6
]}

van Deutekom, J. ^{[6
]}

机构：

[1] Leiden Univ, Dept Human Genet, Med Ctr, NL-2300 RA Leiden, Netherlands

[2] Leiden Univ, Dept Clin Genet, Med Ctr, Leiden, Netherlands

[3] Univ Hosp Leuven, Dept Pediat Neurol, Louvain, Belgium

[4] Univ Gothenburg, Dept Pediat, Gothenburg, Sweden

[5] Leiden Univ, Dept Neurol, Med Ctr, Leiden, Netherlands

[6] Prosensa Therapeut, Leiden, Netherlands

来源：

EUROPEAN JOURNAL OF NEUROLOGY | 2011年 / 18卷

关键词：

D O I：

暂无

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

引用

页码：7 / 7

页数：1

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