Abatacept is useful in autoimmune cytopenia with immunopathologic manifestations caused by CTLA-4 defects

被引:13
|
作者
Dhunputh, C. [1 ,2 ]
Ducassou, S. [1 ,2 ]
Fernandes, H. [2 ]
Picard, Capucine [3 ,4 ]
Rieux-Laucat, Frederic
Viallard, J. -F. [5 ]
Lazaro, E. [5 ]
Hermine, O. [6 ]
Jouvray, M. [7 ]
Machelard, I. [8 ]
Lambilliotte, A. [9 ]
Malphettes, M. [10 ]
Moshous, D. [11 ]
Neven, B. [11 ]
Gauthier, A. [12 ,13 ]
Garnier, N.
Leblanc, T. [14 ]
Landman-Parker, J. [15 ]
Leverger, G. [15 ]
Aladjidi, N. [1 ,2 ]
机构
[1] Bordeaux Univ Hosp, INSERM Plurithemat CIC CICP, Pediatr Hematoimmunol Ctr Invest Clin CIC, Bordeaux, France
[2] Bordeaux Univ Hosp, Ctr Reference Natl Cytopenies Autoimmunes Enfant, Bordeaux, France
[3] Univ Paris, APHP, Necker Hosp Sick Children, Study Ctr Primary Immunodeficiencies, Paris, France
[4] Inst Imagine, INSERM, Unite Mixte Rech UMR 1163, Lab Immunogenet Pediat Autoimmune Dis, Paris, France
[5] Bordeaux Univ Hosp, Dept Internal Med & Infect Dis, Bordeaux, France
[6] Necker Enfants Malades Univ Hosp, AP HP, Hematol Unit, Paris, France
[7] Hosp Arras, Dept Internal Med, Arras, France
[8] Hosp Bayonne, Dept Internal Med, Bayonne, France
[9] Lille Univ Hosp, Dept Pediat Hematol, Lille, France
[10] St Louis Univ Hosp, AP HP, Clin Immunol Dept, Paris, France
[11] Necker Enfants Malades Univ Hosp, AP HP, Pediatr Immunohematol & Rheumatol Dept, Paris, France
[12] Hosp Civils Lyon, Pediatr Hematol & Oncol Inst, Lyon, France
[13] Univ Lyon, Univ Claude Bernard Lyon 1, Team Vascular Biol & Red Blood Cell, Lab Interuniversitaire Biol Motricit,EA7424, Lyon, France
[14] Robert Debre Univ Hosp, AP HP, Pediatr Hematol & Immunol Dept, Paris, France
[15] Armand Trousseau Univ Hosp, AP HP, Pediatr Oncol Immunol Hematol Unit, Paris, France
关键词
RHEUMATOID-ARTHRITIS; IMMUNE DYSREGULATION; SAFETY;
D O I
10.1182/blood.2021013496
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:300 / 304
页数:5
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