Immune Responses to Adeno-Associated Virus-Mediated CRISPR Therapy

被引：1
|
作者：
Keeler, Allison M. [1 ,2 ,3 ]
机构：
[1] Univ Massachusetts, Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA 01605 USA
[2] Univ Massachusetts, Chan Med Sch, Dept Pediat, Worcester, MA 01605 USA
[3] Univ Massachusetts, Chan Med Sch, NeuroNexus Inst, Worcester, MA 01605 USA
来源：
HUMAN GENE THERAPY | 2021年 / 32卷 / 23-24期
关键词：
T-CELL RESPONSES; ALIPOGENE TIPARVOVEC AAV1-LPLS447X; CLINICAL-TRIAL; ALPHA-GLUCOSIDASE; GENE-THERAPY; VECTOR; DYSTROPHY; SAFETY;
D O I：
10.1089/hum.2021.29193.amk
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：1430 / 1432
页数：3
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