Immune Responses to Adeno-Associated Virus-Mediated CRISPR Therapy

被引：1

作者：

Keeler, Allison M. ^{[1
,2
,3
]}

机构：

[1] Univ Massachusetts, Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA 01605 USA

[2] Univ Massachusetts, Chan Med Sch, Dept Pediat, Worcester, MA 01605 USA

[3] Univ Massachusetts, Chan Med Sch, NeuroNexus Inst, Worcester, MA 01605 USA

来源：

HUMAN GENE THERAPY | 2021年 / 32卷 / 23-24期

关键词：

T-CELL RESPONSES; ALIPOGENE TIPARVOVEC AAV1-LPLS447X; CLINICAL-TRIAL; ALPHA-GLUCOSIDASE; GENE-THERAPY; VECTOR; DYSTROPHY; SAFETY;

D O I：

10.1089/hum.2021.29193.amk

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：1430 / 1432

页数：3

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