Antisense Oligonucleotide Therapy for Lafora Disease

被引：0
作者：
Ahonen, Saija [1 ]
Grossman, Tamar [2 ]
Turnbull, Julie [1 ]
Kordasiewicz, Holly [2 ]
Katz, Melanie [2 ]
McCaleb, Michael [2 ]
Wang, Peixiang [1 ]
Zhao, Xiaochu [1 ]
Minassian, Berge [3 ]
机构：
[1] Hosp Sick Children, Toronto, ON, Canada
[2] Ionis Pharmaceut, San Diego, CA USA
[3] Univ Texas Southwestern Med Ctr Dallas, Dallas, TX 75390 USA
来源：
NEUROLOGY | 2018年 / 90卷
关键词：
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
S53.005
引用
收藏
页数：2
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