Lentiviral gene therapy of RAG1 SCID: risks and implications for treatment

被引：0
|
作者：
van Til, N. P. [1 ]
Sarwari, R. [1 ]
Visser, T. P. [1 ]
de Boer, H. [1 ]
Li, Y. [1 ]
Hauer, J. [2 ,3 ]
Lagresle-Peyrou, C. [2 ,3 ]
Danos, O. [3 ,4 ]
Jollet, A. [3 ,4 ]
Zhang, F. [5 ]
Thrasher, A. [5 ]
Cassani, B. [6 ]
Verstegen, M. [1 ]
Villa, A. [7 ]
Cavazzana-Calvo, M. [2 ,3 ]
Wagemaker, G. [1 ]
机构：
[1] Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, Netherlands
[2] Univ Paris 05, INSERM, U768, Paris, France
[3] Hop Necker Enfants Malad, Paris, France
[4] Univ Paris 05, INSERM, U781, Paris, France
[5] UCL Inst Child Hlth, Mol Immunol Unit, London, England
[6] Fdn Humanitas Ric, Milan, Italy
[7] CNR ITB, Telethon Inst Gene Therapy HSR, Milan, Italy
来源：
HUMAN GENE THERAPY | 2010年 / 21卷 / 10期
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D O I：
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中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
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页码：1445 / 1445
页数：1
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