Safety and Efficacy of Emapalumab in Pediatric Patients with Primary Hemophagocytic Lymphohistiocytosis

被引:14
作者
Locatelli, Franco [1 ]
Jordan, Michael B. [2 ]
Allen, Carl E. [3 ]
Cesaro, Simone [4 ]
Rizzari, Carmelo [5 ]
Rao, Anupama [6 ]
Degar, Barbara [7 ]
Garrington, Timothy [8 ]
Sevilla, Julian [9 ]
Putti, Maria Caterina [10 ]
Fagioli, Franca [11 ]
Ahlmann, Martina [12 ]
Dapena, Jose-Luis [13 ]
Grom, Alexei A. [14 ]
De Benedetti, Fabrizio [15 ]
Ferlin, Walter Giovanni [16 ]
Ballabio, Maria [16 ]
De Min, Cristina [16 ]
机构
[1] Bambino Gesu Childrens Hosp IRCCS, Dept Oncohematol, Rome, Italy
[2] Cincinnati Childrens Hosp Med Ctr, Dept Pediat, Div Immunobiol, Cincinnati, OH 45229 USA
[3] Texas Childrens Hosp, Texas Childrens Canc Ctr, Dept Pediat, Houston, TX 77030 USA
[4] Univ Hosp Verona, Dept Pediat Oncohematol, Verona, Italy
[5] Univ Milano Bicocca, San Gerardo Hosp, Dept Pediat, Monza, Italy
[6] Great Ormond St Hosp Sick Children, Dept Haematol, London, England
[7] Dana Farber Canc Inst, Div Pediat Hematol Oncol, Boston, MA 02115 USA
[8] Childrens Hosp Colorado, Ctr Canc & Blood Disorders, Aurora, CO USA
[9] Univ Children Hosp Nino Jesus, Dept Pediat Oncohematol, Madrid, Spain
[10] Univ Padua, Dept Pediat, Div Pediat Hematol & Oncol, Padua, Italy
[11] Regina Margherita S Anna Hosp, Div Pediat Oncohematol, Turin, Italy
[12] Univ Childrens Hosp Muenster, Dept Pediat Hematol & Oncol, Munster, Germany
[13] Univ Hosp Vall dHebron, Dept Pediat Hematol & Oncol, Barcelona, Spain
[14] Cincinnati Childrens Hosp Med Ctr, Div Rheumatol, Cincinnati, OH 45229 USA
[15] Bambino Gesu Childrens Hosp IRCCS, Div Rheumatol, Rome, Italy
[16] Novimmune SA, Geneva, Switzerland
关键词
D O I
10.1182/blood-2018-120810
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
LBA-6
引用
收藏
页数:3
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