Hemophilia as a blueprint for gene therapy

被引：13
|
作者：
Ragni, Margaret V. [1 ,2 ]
机构：
[1] Univ Pittsburgh, Med Ctr, Dept Med, Div Hematol Oncol, Pittsburgh, PA 15260 USA
[2] Hemophilia Ctr Western, Pittsburgh, PA 15213 USA
来源：
SCIENCE | 2021年 / 374卷 / 6563期
基金：
美国国家卫生研究院;
关键词：
EMICIZUMAB;
D O I：
10.1126/science.abg0856
中图分类号：
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号：
07 ; 0710 ; 09 ;
摘要：
Advances in hemophilia gene therapy could enable progress in other inherited disorders
引用
收藏
页码：40 / 41
页数：2
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