NON-VIRAL GENE EDITING APPROACHES TO GENETICALLY AUGMENT AND CORRECT CYSTIC FIBROSIS USING MUCUS PENETRATING PEPTIDE NANOPARTICLES

被引:0
作者
Savage, Aaron M. [1 ]
Eltaher, Hoda [1 ]
Suk, Jung Soo [2 ]
Dixon, James E. [1 ]
机构
[1] Univ Nottingham, Nottingham, England
[2] Johns Hopkins Univ, Baltimore, MD USA
关键词
Cystic Fibrosis; Gene Therapy;
D O I
暂无
中图分类号
Q813 [细胞工程];
学科分类号
摘要
1917
引用
收藏
页码:S541 / S541
页数:1
相关论文
共 2 条
  • [1] Highly efficient delivery of functional cargoes by the synergistic effect of GAG binding motifs and cell-penetrating peptides
    Dixon, James E.
    Osman, Gizem
    Morris, Gavin E.
    Markides, Hareklea
    Rotherham, Michael
    Bayoussef, Zahia
    El Haj, Alicia J.
    Denning, Chris
    Shakesheff, Kevin M.
    [J]. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 2016, 113 (03) : E291 - E299
  • [2] Osman Gizem, 2018, J CONTROL RELEASE, V285, P35