In vivo generated hematopoietic stem cells from genome edited induced pluripotent stem cells are functional in platelet-targeted gene therapy of murine hemophilia A

被引：10

作者：

Wang, Dawei ^{[1
,2
]}

Zhang, Guowei ^{[1
,3
]}

Gu, Junjie ^{[4
,5
]}

Shao, Xiaohu ^{[1
]}

Dai, Yuting ^{[1
]}

Li, Jianfeng ^{[1
]}

Pan, Xiaohong ^{[1
]}

Yao, Shuxian ^{[1
]}

Xu, Aining ^{[1
]}

Jin, Ying ^{[4
,5
]}

Huang, Jinyan ^{[1
]}

Shi, Qizhen ^{[6
]}

Zhu, Jiang ^{[1
]}

Xi, Xiaodong ^{[1
]}

Chen, Zhu ^{[1
,2
]}

Chen, Saijuan ^{[1
,2
]}

机构：

[1] Shanghai Jiao Tong Univ, Sch Med, Ruijin Hosp, State Key Lab Med Genom,Shanghai Inst Hematol, Shanghai, Peoples R China

[2] Shanghai Jiao Tong Univ, Sch Med, Natl Res Ctr Translat Med, Shanghai, Peoples R China

[3] Hangzhou Normal Univ, Sch Med, Key Lab Aging & Canc Biol Zhejiang Prov, Hangzhou, Peoples R China

[4] Chinese Acad Sci, Shanghai Inst Biol Sci, Ctr Excellence Mol & Cell Sci, Key Lab Stem Cell Biol,Inst Hlth Sci, Shanghai, Peoples R China

[5] Shanghai Jiao Tong Univ, Sch Med, Shanghai, Peoples R China

[6] Med Coll Wisconsin, Dept Pediat, 8701 Watertown Plank Rd, Milwaukee, WI 53226 USA

来源：

HAEMATOLOGICA | 2020年 / 105卷 / 04期

关键词：

PROGENITOR CELLS;

D O I：

10.3324/haematol.2019.219089

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页数：5

共 15 条

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