Neonatal delivery of a retroviral vector expressing canine β-glucuronidase results in long-term gene expression and marked improvement in the clinical manifestations in mucopolysaccharidosis VII dogs.

被引：0
|
作者：
Xu, LF
Ponder, KP
Melniczek, JR
Weil, MA
Haskins, ME
机构：
[1] Washington Univ, Sch Med, Dept Internal Med & Biochem & Mol Biophys, St Louis, MO USA
[2] Univ Penn, Sch Vet Med, Dept Pathobiol, Philadelphia, PA 19104 USA
来源：
BLOOD | 2001年 / 98卷 / 11期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
2899
引用
收藏
页码：693A / 693A
页数：1
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