Redosing Adeno-Associated Virus Gene Therapy to the Central Nervous System

被引：5
作者：
McElroy, Abigail [1 ,2 ]
Sena-Esteves, Miguel [1 ,2 ,3 ]
Arjomandnejad, Motahareh [1 ,2 ]
Keeler, Allison M. M. [1 ,2 ,4 ]
Gray-Edwards, Heather L. L. [1 ,2 ,5 ,6 ,7 ]
机构：
[1] UMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
[2] UMass Chan Med Sch, Li Weibo Inst Rare Dis Res, Worcester, MA USA
[3] UMass Chan Med Sch, Dept Neurol, Worcester, MA USA
[4] UMass Chan Med Sch, Dept Pediat, Worcester, MA USA
[5] UMass Chan Med Sch, Dept Radiol, Worcester, MA USA
[6] UMass Chan Med Sch, Horae Gene Therapy Ctr, 368 Plantat St, Worcester, MA 01605 USA
[7] UMass Chan Med Sch, Li Weibo Inst Rare Dis Res, 368 Plantat St, Worcester, MA 01605 USA
来源：
HUMAN GENE THERAPY | 2022年 / 33卷 / 17-18期
关键词：
central nervous system; gene therapy; AAV; NEUTRALIZING ANTIBODIES; TRANSGENE EXPRESSION; SKELETAL-MUSCLE; ADULT MICE; BRAIN; AAV; VECTORS; DELIVERY; TURNOVER; ROUTES;
D O I：
10.1089/hum.2022.170
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
[No abstract available]
引用
收藏
页码：889 / 892
页数：4
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