Redosing Adeno-Associated Virus Gene Therapy to the Central Nervous System
被引:5
作者:
McElroy, Abigail
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机构:
UMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
UMass Chan Med Sch, Li Weibo Inst Rare Dis Res, Worcester, MA USAUMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
McElroy, Abigail
[1
,2
]
Sena-Esteves, Miguel
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机构:
UMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
UMass Chan Med Sch, Li Weibo Inst Rare Dis Res, Worcester, MA USA
UMass Chan Med Sch, Dept Neurol, Worcester, MA USAUMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
Sena-Esteves, Miguel
[1
,2
,3
]
Arjomandnejad, Motahareh
论文数: 0引用数: 0
h-index: 0
机构:
UMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
UMass Chan Med Sch, Li Weibo Inst Rare Dis Res, Worcester, MA USAUMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
Arjomandnejad, Motahareh
[1
,2
]
Keeler, Allison M. M.
论文数: 0引用数: 0
h-index: 0
机构:
UMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
UMass Chan Med Sch, Li Weibo Inst Rare Dis Res, Worcester, MA USA
UMass Chan Med Sch, Dept Pediat, Worcester, MA USAUMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
Keeler, Allison M. M.
[1
,2
,4
]
Gray-Edwards, Heather L. L.
论文数: 0引用数: 0
h-index: 0
机构:
UMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
UMass Chan Med Sch, Li Weibo Inst Rare Dis Res, Worcester, MA USA
UMass Chan Med Sch, Dept Radiol, Worcester, MA USA
UMass Chan Med Sch, Horae Gene Therapy Ctr, 368 Plantat St, Worcester, MA 01605 USA
UMass Chan Med Sch, Li Weibo Inst Rare Dis Res, 368 Plantat St, Worcester, MA 01605 USAUMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
Gray-Edwards, Heather L. L.
[1
,2
,5
,6
,7
]
机构:
[1] UMass Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA USA
[2] UMass Chan Med Sch, Li Weibo Inst Rare Dis Res, Worcester, MA USA
[3] UMass Chan Med Sch, Dept Neurol, Worcester, MA USA
[4] UMass Chan Med Sch, Dept Pediat, Worcester, MA USA
[5] UMass Chan Med Sch, Dept Radiol, Worcester, MA USA
[6] UMass Chan Med Sch, Horae Gene Therapy Ctr, 368 Plantat St, Worcester, MA 01605 USA
[7] UMass Chan Med Sch, Li Weibo Inst Rare Dis Res, 368 Plantat St, Worcester, MA 01605 USA
机构:
UCLA, David Geffen Sch Med, Intellectual & Dev Disabil Res Ctr, Dept Mol & Med Pharmacol, Los Angeles, CA 90095 USA
UCLA, Intellectual & Dev Disabil Res Ctr, David GeffenSchool Med, Surg, Los Angeles, CA 90095 USATaysha Gene Therapies, Dallas, TX USA
机构:
NHGRI, Organ Acid Res Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA
NIH, Med Res Scholars Program, Bldg 10, Bethesda, MD 20892 USA
Case Western Reserve Univ, Lerner Coll Med, Cleveland Clin, Cleveland, OH 44106 USANHGRI, Organ Acid Res Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA
May, Francis J.
Head, PamelaSara E.
论文数: 0引用数: 0
h-index: 0
机构:
NHGRI, Organ Acid Res Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USANHGRI, Organ Acid Res Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA
Head, PamelaSara E.
Venturoni, Leah E.
论文数: 0引用数: 0
h-index: 0
机构:
NHGRI, Organ Acid Res Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USANHGRI, Organ Acid Res Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA
Venturoni, Leah E.
Chandler, Randy J.
论文数: 0引用数: 0
h-index: 0
机构:
NHGRI, Organ Acid Res Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USANHGRI, Organ Acid Res Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA
Chandler, Randy J.
Venditti, Charles P.
论文数: 0引用数: 0
h-index: 0
机构:
NHGRI, Organ Acid Res Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USANHGRI, Organ Acid Res Sect, Med Genom & Metab Genet Branch, NIH, Bethesda, MD 20892 USA
机构:
Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USAUniv Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA
Samelson-Jones, Benjamin J.
George, Lindsey A.
论文数: 0引用数: 0
h-index: 0
机构:
Univ Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Div Hematol, Philadelphia, PA 19104 USA
Childrens Hosp Philadelphia, Raymond G Perelman Ctr Cellular & Mol Therapeut, Philadelphia, PA 19104 USAUniv Penn, Dept Pediat, Perelman Sch Med, Philadelphia, PA 19104 USA
机构:
Univ Massachusetts, Dept Neurosurg, Chan Med Sch, 55 N Lake Ave, Worcester, MA 01655 USA
Univ Massachusetts, Horae Gene Therapy Ctr, Chan Med Sch, 368 Plantat St, Worcester, MA 01605 USAUniv Massachusetts, Dept Neurosurg, Chan Med Sch, 55 N Lake Ave, Worcester, MA 01655 USA
Daci, Rrita
Flotte, Terence R.
论文数: 0引用数: 0
h-index: 0
机构:
Univ Massachusetts, Horae Gene Therapy Ctr, Chan Med Sch, 368 Plantat St, Worcester, MA 01605 USA
Univ Massachusetts, Dept Pediat, Chan Med Sch, 55 N Lake Ave, Worcester, MA 01655 USAUniv Massachusetts, Dept Neurosurg, Chan Med Sch, 55 N Lake Ave, Worcester, MA 01655 USA
机构:
Univ Massachusetts, Morningside Grad Sch Biomed Sci, Grad Program Neurosci, Chan Med Sch, Amherst, MA 01003 USA
Univ Massachusetts, Chan Med Sch, Dept Neurol, Amherst, MA USA
Univ Massachusetts, Horae Gene Therapy Ctr, Chan Med Sch, Amherst, MA 01003 USAUniv Massachusetts, Morningside Grad Sch Biomed Sci, Grad Program Neurosci, Chan Med Sch, Amherst, MA 01003 USA
Harkins, Ashley L.
Ambegaokar, Prajakta P.
论文数: 0引用数: 0
h-index: 0
机构:
Univ Massachusetts, Morningside Grad Sch Biomed Sci, Chan Med Sch, Grad Program Translat Sci, Amherst, MA 01003 USA
Univ Massachusetts, Horae Gene Therapy Ctr, Chan Med Sch, Amherst, MA 01003 USAUniv Massachusetts, Morningside Grad Sch Biomed Sci, Grad Program Neurosci, Chan Med Sch, Amherst, MA 01003 USA
Ambegaokar, Prajakta P.
Keeler, Allison M.
论文数: 0引用数: 0
h-index: 0
机构:
Univ Massachusetts, Morningside Grad Sch Biomed Sci, Grad Program Neurosci, Chan Med Sch, Amherst, MA 01003 USA
Univ Massachusetts, Morningside Grad Sch Biomed Sci, Chan Med Sch, Grad Program Translat Sci, Amherst, MA 01003 USA
Univ Massachusetts, NeuroNexus Inst, Chan Med Sch, Amherst, MA 01003 USA
Univ Massachusetts, Chan Med Sch, Dept Pediat, Amherst, MA 01003 USA
Univ Massachusetts, Horae Gene Therapy Ctr, Chan Med Sch, Amherst, MA 01003 USAUniv Massachusetts, Morningside Grad Sch Biomed Sci, Grad Program Neurosci, Chan Med Sch, Amherst, MA 01003 USA