RESTORATION OF CFTR FUNCTION BY ANTISENSE OLIGONUCLEOTIDE SPLICING MODULATION

被引：0
|
作者：
Oren, Y. [1 ,2 ]
Tur-Sinai, Irony M. [1 ]
Ozeri-Galai, E. [1 ,2 ]
Avizur, O. [1 ,2 ]
Mutyam, V [3 ]
Wilton, S. [4 ]
Rowe, S. M. [3 ]
Kerem, B. [1 ]
机构：
[1] Hebrew Univ Jerusalem, Genet, Jerusalem, Israel
[2] SpliSense, Jerusalem, Israel
[3] Univ Alabama Birmingham, Birmingham, AL USA
[4] Univ Western Australia, Ctr Neuromuscular & Neurol Disorders, Crawley, WA, Australia
来源：
PEDIATRIC PULMONOLOGY | 2017年 / 52卷
关键词：
D O I：
暂无
中图分类号：
R72 [儿科学];
学科分类号：
100202 ;
摘要：
261
引用
收藏
页码：S313 / S313
页数：1
相关论文
共 50 条
  • [21] Screening for antisense modulation of dystrophin pre-mRNA splicing
    Dickson, G
    Hill, V
    Graham, IR
    NEUROMUSCULAR DISORDERS, 2002, 12 : S67 - S70
  • [22] In vivo modulation of the splicing pattern of CFTR exon 9 by cellular and viral splicing factors.
    Nissim-Rafinia, M
    Chiba-Falek, O
    Kerem, E
    Kerem, B
    AMERICAN JOURNAL OF HUMAN GENETICS, 1999, 65 (04) : A502 - A502
  • [23] Progress toward therapy with antisense-mediated splicing modulation
    Du, Liutao
    Gatti, Richard A.
    CURRENT OPINION IN MOLECULAR THERAPEUTICS, 2009, 11 (02) : 116 - 123
  • [24] An antisense oligonucleotide efficiently suppresses splicing of an alternative exon in vascular smooth muscle in vivo
    de Angelis, Celio Damacena
    Meddeb, Mariam
    Chen, Nelson
    Fisher, Steven A.
    AMERICAN JOURNAL OF PHYSIOLOGY-HEART AND CIRCULATORY PHYSIOLOGY, 2024, 326 (03): : H860 - H869
  • [25] Antisense oligonucleotide-based rescue of complex splicing defects in ABCA4
    Corradi, Zelia
    De Rooij, Laura
    Hitti-Malin, Rebekkah J.
    Garanto, Alejandro
    Collin, Rob W. J.
    Cremers, Frans P.
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2022, 63 (07)
  • [26] Correction of aberrant splicing of the cystic fibrosis transmembrane conductance regulator (CFTR) gene by Antisense Oligonucleotides
    J Biol Chem, 51 (36193-36199):
  • [27] Correction of aberrant splicing of the cystic fibrosis transmembrane conductance regulator (CFTR) gene by antisense oligonucleotides
    Friedman, KJ
    Kole, J
    Cohn, JA
    Knowles, MR
    Silverman, LM
    Kole, R
    JOURNAL OF BIOLOGICAL CHEMISTRY, 1999, 274 (51) : 36193 - 36199
  • [28] An antisense oligonucleotide primer
    Hogrefe, RI
    ANTISENSE & NUCLEIC ACID DRUG DEVELOPMENT, 1999, 9 (04): : 351 - 357
  • [29] RNA Trans-Splicing Modulation via Antisense Molecule Interference
    Liemberger, Bernadette
    Hofbauer, Josefina Pinon
    Wally, Verena
    Arzt, Claudia
    Hainzl, Stefan
    Kocher, Thomas
    Murauer, Eva M.
    Bauer, Johann W.
    Reichelt, Julia
    Koller, Ulrich
    INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, 2018, 19 (03)
  • [30] Antisense oligonucleotide therapeutics
    Cook, PD
    ABSTRACTS OF PAPERS OF THE AMERICAN CHEMICAL SOCIETY, 1999, 217 : U219 - U219
12345