New therapies for lysosomal storage disorders

被引:0
作者
Jones, Simon [1 ]
机构
[1] Univ Manchester, Manchester Acad Hlth Sci Ctr, Cent Manchester Univ Hosp NHS Fdn Trust, St Marys Hosp, Manchester M13 9PL, Lancs, England
关键词
D O I
暂无
中图分类号
Q3 [遗传学];
学科分类号
071007 ; 090102 ;
摘要
引用
收藏
页码:S44 / S44
页数:1
相关论文
共 50 条
  • [21] Lysosomal Storage Disorders
    Stulnig, T.
    AUSTRIAN JOURNAL OF CLINICAL ENDOCRINOLOGY AND METABOLISM, 2011, 4 (02): : 22 - 26
  • [22] LYSOSOMAL STORAGE DISORDERS
    ZLOTOGORA, J
    BACH, G
    BIOMEDICINE & PHARMACOTHERAPY, 1986, 40 (08) : 314 - 314
  • [23] Lysosomal storage disorders
    Beck, M.
    MONATSSCHRIFT KINDERHEILKUNDE, 2007, 155 (07) : 653 - 661
  • [24] Lysosomal storage disorders
    Michelle Grayson
    Nature, 2016, 537 : S145 - S145
  • [25] LYSOSOMAL STORAGE DISORDERS
    Grayson, Michelle
    NATURE, 2016, 537 (7621) : S145 - S145
  • [27] Delayed infusion reactions associated with enzyme replacement therapies for lysosomal storage disorders
    Utz, Jeanine
    Doyen, Colleen
    Whitley, Chester B.
    MOLECULAR GENETICS AND METABOLISM, 2008, 93 (02) : S40 - S40
  • [28] Combined Therapies for Lysosomal Storage Diseases
    Gabig-Ciminska, M.
    Jakobkiewicz-Banecka, J.
    Malinowska, M.
    Kloska, A.
    Piotrowska, E.
    Chmielarz, I.
    Moskot, M.
    Wegrzyn, A.
    Wegrzyn, G.
    CURRENT MOLECULAR MEDICINE, 2015, 15 (08) : 746 - 771
  • [29] Autophagy in lysosomal storage disorders
    Lieberman, Andrew P.
    Puertollano, Rosa
    Raben, Nina
    Slaugenhaupt, Susan
    Walkley, Steven U.
    Ballabio, Andrea
    AUTOPHAGY, 2012, 8 (05) : 719 - 730
  • [30] Sphingolipid lysosomal storage disorders
    Platt, Frances M.
    NATURE, 2014, 510 (7503) : 68 - 75